The ANZCTR website will be unavailable from 1pm until 3pm (AEDT) on Wednesday the 30th of October for website maintenance. Please be sure to log out of the system in order to avoid any loss of data.

The safety and scientific validity of this study is the responsibility of the study sponsor and investigators. Listing a study does not mean it has been endorsed by the ANZCTR. Before participating in a study, talk to your health care provider and refer to this information for consumers
Trial details imported from ClinicalTrials.gov

For full trial details, please see the original record at https://clinicaltrials.gov/study/NCT03643965




Registration number
NCT03643965
Ethics application status
Date submitted
8/08/2018
Date registered
23/08/2018

Titles & IDs
Public title
Efficacy and Safety of Nefecon in Patients With Primary IgA (Immunoglobulin A) Nephropathy
Scientific title
A Randomized, Double-blind, Placebo Controlled Study to Evaluate Efficacy and Safety of Nefecon in Patients With Primary IgA (Immunoglobulin A) Nephropathy at Risk of Progressing to End-stage Renal Disease (NefIgArd)
Secondary ID [1] 0 0
Nef-301
Universal Trial Number (UTN)
Trial acronym
Nefigard
Linked study record

Health condition
Health condition(s) or problem(s) studied:
Primary IgA Nephropathy 0 0
Condition category
Condition code
Renal and Urogenital 0 0 0 0
Kidney disease
Inflammatory and Immune System 0 0 0 0
Autoimmune diseases

Intervention/exposure
Study type
Interventional
Description of intervention(s) / exposure
Treatment: Drugs - Nefecon
Treatment: Drugs - Placebo oral capsule

Experimental: Nefecon - Nefecon 16 mg once daily by mouth for 9 months.

Placebo comparator: Placebo oral capsule - Placebo oral capsule once daily by mouth for 9 months.


Treatment: Drugs: Nefecon
Nefecon 16 mg for daily administration by mouth for 9 months.

Treatment: Drugs: Placebo oral capsule
Placebo capsules for daily administration by mouth for 9 months.

Intervention code [1] 0 0
Treatment: Drugs
Comparator / control treatment
Control group

Outcomes
Primary outcome [1] 0 0
Change in Proteinuria, measured as Urine Protein to creatinine ratio (UPCR).
Timepoint [1] 0 0
9 months
Primary outcome [2] 0 0
Renal function measured as estimated glomerular filtration rate (eGFR)
Timepoint [2] 0 0
Up to 2 years
Secondary outcome [1] 0 0
The incidence of treatment-emergent adverse events.
Timepoint [1] 0 0
From enrollment and up to 2 years
Secondary outcome [2] 0 0
Renal function
Timepoint [2] 0 0
Up to 2 years

Eligibility
Key inclusion criteria
1. Female or male patients =18 years
2. Biopsy-verified IgA nephropathy
3. Stable dose of RAS inhibitor therapy (ACEIs and/or ARBs) at the maximum allowed dose or Maximum Tolerated Dose (MTD) according to the 2012 KDIGO (Kidney Disease: Improving Global Outcomes) guidelines
4. Urine protein creatinine ratio =1 g/24hr
5. eGFR =35 mL/min per 1.73 m2 and =90 mL/min per 1.73 m2 using the Chronic Kidney Diseae Epidemiology Collaboration (CKD-EPI) formula
6. Willing and able to give informed consent
Minimum age
18 Years
Maximum age
No limit
Sex
Both males and females
Can healthy volunteers participate?
No
Key exclusion criteria
1. Systemic diseases that may cause mesangial IgA deposition.
2. Patients who have undergone a kidney transplant.
3. Patients with acute or chronic infectious disease including hepatitis, tuberculosis, human immunodeficiency virus (HIV), and chronic urinary tract infections.
4. Patients with liver cirrhosis, as assessed by the Investigator.
5. Patients with a diagnosis of type 1 or type 2 diabetes mellitus which is poorly controlled.
6. Patients with history of unstable angina, class III or IV congestive heart failure, and/or clinically significant arrhythmia, as judged by the Investigator;
7. Patients with unacceptable blood pressure control defined as a blood pressure consistently above national guidelines for proteinuric renal disease, as assessed by the Investigator
8. Patients with diagnosed malignancy within the past 5 years.

Study design
Purpose of the study
Treatment
Allocation to intervention
Randomised controlled trial
Procedure for enrolling a subject and allocating the treatment (allocation concealment procedures)
Methods used to generate the sequence in which subjects will be randomised (sequence generation)
Masking / blinding
Blinded (masking used)
Who is / are masked / blinded?
The people receiving the treatment/s
The people administering the treatment/s
The people assessing the outcomes
The people analysing the results/data
Intervention assignment
Parallel
Other design features
Phase
Phase 3
Type of endpoint/s
Statistical methods / analysis

Recruitment
Recruitment status
Completed
Data analysis
Reason for early stopping/withdrawal
Other reasons
Date of first participant enrolment
Anticipated
Actual
Date of last participant enrolment
Anticipated
Actual
Date of last data collection
Anticipated
Actual
Sample size
Target
Accrual to date
Final
Recruitment in Australia
Recruitment state(s)
VIC
Recruitment hospital [1] 0 0
Monash Medical Centre - Clayton
Recruitment hospital [2] 0 0
Royal Adelaide Hospital, Port Rd. - Adelaide
Recruitment hospital [3] 0 0
Box Hill Hospital, Dept of Renal Medicine, Arnold Str 5 - Box Hill
Recruitment hospital [4] 0 0
Austin Health, Dept of Nephrology, 145 Studley Rd. - Heidelberg
Recruitment hospital [5] 0 0
Melbourne Health, Royal Melbourne Hospital, Dept of Nephrology,Grattan Str. - Parkville
Recruitment hospital [6] 0 0
Prince of Wales Hospital, Nephrology Dept, Parkes 3 West - Randwick
Recruitment hospital [7] 0 0
Western Health, Western Hospital-Sunshine Hospital, 176 Furlong Rd, Level 3, WHCRE Building - St Albans
Recruitment hospital [8] 0 0
Westmead Hospital, Dept of Renal Medicine, Hawkesbury Rd. - Westmead
Recruitment hospital [9] 0 0
Metro South Hospital and Health Service via Princess Alexandra Hospital, Dept of Nephrology, 199 Ipswich Rd. - Woolloongabba
Recruitment postcode(s) [1] 0 0
3168 - Clayton
Recruitment postcode(s) [2] 0 0
5000 - Adelaide
Recruitment postcode(s) [3] 0 0
3128 - Box Hill
Recruitment postcode(s) [4] 0 0
3084 - Heidelberg
Recruitment postcode(s) [5] 0 0
3052 - Parkville
Recruitment postcode(s) [6] 0 0
2031 - Randwick
Recruitment postcode(s) [7] 0 0
3021 - St Albans
Recruitment postcode(s) [8] 0 0
2145 - Westmead
Recruitment postcode(s) [9] 0 0
4102 - Woolloongabba
Recruitment outside Australia
Country [1] 0 0
United States of America
State/province [1] 0 0
Alabama
Country [2] 0 0
United States of America
State/province [2] 0 0
Arizona
Country [3] 0 0
United States of America
State/province [3] 0 0
California
Country [4] 0 0
United States of America
State/province [4] 0 0
Colorado
Country [5] 0 0
United States of America
State/province [5] 0 0
Connecticut
Country [6] 0 0
United States of America
State/province [6] 0 0
District of Columbia
Country [7] 0 0
United States of America
State/province [7] 0 0
Florida
Country [8] 0 0
United States of America
State/province [8] 0 0
Illinois
Country [9] 0 0
United States of America
State/province [9] 0 0
Kentucky
Country [10] 0 0
United States of America
State/province [10] 0 0
Massachusetts
Country [11] 0 0
United States of America
State/province [11] 0 0
Minnesota
Country [12] 0 0
United States of America
State/province [12] 0 0
Missouri
Country [13] 0 0
United States of America
State/province [13] 0 0
New York
Country [14] 0 0
United States of America
State/province [14] 0 0
North Carolina
Country [15] 0 0
United States of America
State/province [15] 0 0
Ohio
Country [16] 0 0
United States of America
State/province [16] 0 0
Oregon
Country [17] 0 0
United States of America
State/province [17] 0 0
Pennsylvania
Country [18] 0 0
United States of America
State/province [18] 0 0
Tennessee
Country [19] 0 0
United States of America
State/province [19] 0 0
Texas
Country [20] 0 0
United States of America
State/province [20] 0 0
Vermont
Country [21] 0 0
Argentina
State/province [21] 0 0
Capital federal
Country [22] 0 0
Argentina
State/province [22] 0 0
Córdoba
Country [23] 0 0
Argentina
State/province [23] 0 0
Pilar
Country [24] 0 0
Argentina
State/province [24] 0 0
Santa Fe
Country [25] 0 0
Belarus
State/province [25] 0 0
Brest
Country [26] 0 0
Belarus
State/province [26] 0 0
Gomel
Country [27] 0 0
Belarus
State/province [27] 0 0
Grodno
Country [28] 0 0
Belarus
State/province [28] 0 0
Minsk
Country [29] 0 0
Belgium
State/province [29] 0 0
Brussels
Country [30] 0 0
Belgium
State/province [30] 0 0
Brussel
Country [31] 0 0
Belgium
State/province [31] 0 0
Gent
Country [32] 0 0
Belgium
State/province [32] 0 0
Liège
Country [33] 0 0
Belgium
State/province [33] 0 0
Roeselare
Country [34] 0 0
Canada
State/province [34] 0 0
British Columbia
Country [35] 0 0
Canada
State/province [35] 0 0
Nova Scotia
Country [36] 0 0
Canada
State/province [36] 0 0
Ontario
Country [37] 0 0
Canada
State/province [37] 0 0
Quebec
Country [38] 0 0
Czechia
State/province [38] 0 0
Brno
Country [39] 0 0
Czechia
State/province [39] 0 0
Hradec Králové
Country [40] 0 0
Czechia
State/province [40] 0 0
Olomouc
Country [41] 0 0
Czechia
State/province [41] 0 0
Praha 10
Country [42] 0 0
Czechia
State/province [42] 0 0
Praha 2
Country [43] 0 0
Finland
State/province [43] 0 0
Helsinki
Country [44] 0 0
Finland
State/province [44] 0 0
Jyväskylä
Country [45] 0 0
Finland
State/province [45] 0 0
Tampere
Country [46] 0 0
France
State/province [46] 0 0
Boulogne-sur-Mer
Country [47] 0 0
France
State/province [47] 0 0
Grenoble
Country [48] 0 0
France
State/province [48] 0 0
Montpellier
Country [49] 0 0
France
State/province [49] 0 0
Paris
Country [50] 0 0
France
State/province [50] 0 0
Saint-Priest-en-Jarez
Country [51] 0 0
France
State/province [51] 0 0
Valenciennes
Country [52] 0 0
Germany
State/province [52] 0 0
Aachen
Country [53] 0 0
Germany
State/province [53] 0 0
Dresden
Country [54] 0 0
Germany
State/province [54] 0 0
Erlangen
Country [55] 0 0
Germany
State/province [55] 0 0
Heidelberg
Country [56] 0 0
Germany
State/province [56] 0 0
Lubeck
Country [57] 0 0
Germany
State/province [57] 0 0
Munich
Country [58] 0 0
Germany
State/province [58] 0 0
Regensburg
Country [59] 0 0
Greece
State/province [59] 0 0
Athens
Country [60] 0 0
Greece
State/province [60] 0 0
Heraklion
Country [61] 0 0
Greece
State/province [61] 0 0
Ioánnina
Country [62] 0 0
Greece
State/province [62] 0 0
Larissa
Country [63] 0 0
Greece
State/province [63] 0 0
Níkaia
Country [64] 0 0
Greece
State/province [64] 0 0
Patras
Country [65] 0 0
Greece
State/province [65] 0 0
Thessaloníki
Country [66] 0 0
Italy
State/province [66] 0 0
Bari
Country [67] 0 0
Italy
State/province [67] 0 0
Lecco
Country [68] 0 0
Italy
State/province [68] 0 0
Milano
Country [69] 0 0
Italy
State/province [69] 0 0
Pavia
Country [70] 0 0
Korea, Republic of
State/province [70] 0 0
Busan
Country [71] 0 0
Korea, Republic of
State/province [71] 0 0
Daegu
Country [72] 0 0
Korea, Republic of
State/province [72] 0 0
Daejeon
Country [73] 0 0
Korea, Republic of
State/province [73] 0 0
Gyeonggi-do
Country [74] 0 0
Korea, Republic of
State/province [74] 0 0
Seoul
Country [75] 0 0
Poland
State/province [75] 0 0
Gdansk
Country [76] 0 0
Poland
State/province [76] 0 0
Olsztyn
Country [77] 0 0
Poland
State/province [77] 0 0
Szczecin
Country [78] 0 0
Poland
State/province [78] 0 0
Lódz
Country [79] 0 0
Spain
State/province [79] 0 0
Alcorcón
Country [80] 0 0
Spain
State/province [80] 0 0
Barcelona
Country [81] 0 0
Spain
State/province [81] 0 0
Lleida
Country [82] 0 0
Spain
State/province [82] 0 0
Madrid
Country [83] 0 0
Sweden
State/province [83] 0 0
Göteborg
Country [84] 0 0
Sweden
State/province [84] 0 0
Linköping
Country [85] 0 0
Sweden
State/province [85] 0 0
Stockholm
Country [86] 0 0
Sweden
State/province [86] 0 0
Uppsala
Country [87] 0 0
Taiwan
State/province [87] 0 0
Kaohsiung
Country [88] 0 0
Taiwan
State/province [88] 0 0
Taichung
Country [89] 0 0
Taiwan
State/province [89] 0 0
Tainan
Country [90] 0 0
Turkey
State/province [90] 0 0
Adana
Country [91] 0 0
Turkey
State/province [91] 0 0
Istanbul
Country [92] 0 0
Turkey
State/province [92] 0 0
Izmir
Country [93] 0 0
Turkey
State/province [93] 0 0
Kayseri
Country [94] 0 0
Turkey
State/province [94] 0 0
Kocaeli
Country [95] 0 0
United Kingdom
State/province [95] 0 0
Belfast
Country [96] 0 0
United Kingdom
State/province [96] 0 0
Bristol
Country [97] 0 0
United Kingdom
State/province [97] 0 0
Glasgow
Country [98] 0 0
United Kingdom
State/province [98] 0 0
Gloucester
Country [99] 0 0
United Kingdom
State/province [99] 0 0
Leeds
Country [100] 0 0
United Kingdom
State/province [100] 0 0
Leicester
Country [101] 0 0
United Kingdom
State/province [101] 0 0
London
Country [102] 0 0
United Kingdom
State/province [102] 0 0
Manchester
Country [103] 0 0
United Kingdom
State/province [103] 0 0
Nottingham
Country [104] 0 0
United Kingdom
State/province [104] 0 0
Sheffield

Funding & Sponsors
Primary sponsor type
Commercial sector/industry
Name
Calliditas Therapeutics AB
Address
Country

Ethics approval
Ethics application status

Summary
Brief summary
Trial website
Trial related presentations / publications
Public notes

Contacts
Principal investigator
Name 0 0
Krassimir Mitchev, MD
Address 0 0
Calliditas AB
Country 0 0
Phone 0 0
Fax 0 0
Email 0 0
Contact person for public queries
Name 0 0
Address 0 0
Country 0 0
Phone 0 0
Fax 0 0
Email 0 0
Contact person for scientific queries

Data sharing statement
Will individual participant data (IPD) for this trial be available (including data dictionaries)?
No
No/undecided IPD sharing reason/comment


What supporting documents are/will be available?

No Supporting Document Provided



Results publications and other study-related documents

No documents have been uploaded by study researchers.