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Trial details imported from ClinicalTrials.gov

For full trial details, please see the original record at https://clinicaltrials.gov/study/NCT00621244




Registration number
NCT00621244
Ethics application status
Date submitted
12/02/2008
Date registered
22/02/2008
Date last updated
5/01/2021

Titles & IDs
Public title
A Study of Oral LBH589 in Adult Patients With Advanced Hematological Malignancies
Scientific title
A Phase IA/II, Two-arm, Multi-center, Open-label, Dose-escalation Study of LBH589 Administered Orally Via Different Dosing Schedules in Adult Patients With Advanced Hematological Malignancies
Secondary ID [1] 0 0
2005-003670-26
Secondary ID [2] 0 0
CLBH589B2102
Universal Trial Number (UTN)
Trial acronym
Linked study record

Health condition
Health condition(s) or problem(s) studied:
Lymphoma 0 0
Leukemia 0 0
Multiple Myeloma 0 0
Condition category
Condition code
Cancer 0 0 0 0
Leukaemia - Acute leukaemia
Cancer 0 0 0 0
Leukaemia - Chronic leukaemia

Intervention/exposure
Study type
Interventional
Description of intervention(s) / exposure
Experimental: Arm 1, Group X -

Experimental: Arm 1, Group Y -

Experimental: Arm 2, Group X -

Experimental: Arm 2, Group Y - Panobinostat was administered orally, once-a-day, on Monday-Wednesday-Friday (MWF), every other week, as part of a 28-day treatment cycle. Group Y is a sub-arm, based on disease indication.

Comparator / control treatment
Control group

Outcomes
Primary outcome [1] 0 0
Number of Participants DLT in Arm 1 in Dose Escalation Phase
Timepoint [1] 0 0
Cycle 1 (28-day treatment cycle)
Primary outcome [2] 0 0
Number of Participants DLT in Arm 2 in Dose Escalation Phase
Timepoint [2] 0 0
Cycle 1 (28-day treamtent cycle)
Secondary outcome [1] 0 0
Response as Per Investigator Assessment for Patients With Acute Myelogenous Leukemia (AML)
Timepoint [1] 0 0
3.5 years
Secondary outcome [2] 0 0
Response as Per Investigator Assessment for Patients With Acute Myelogenous Leukemia (AML) in Expansion Phase
Timepoint [2] 0 0
1.2 years
Secondary outcome [3] 0 0
Response as Per Investigator Assessment for Patients With Hodgkin's Lymphoma (HD)
Timepoint [3] 0 0
3.5 years
Secondary outcome [4] 0 0
Response as Per Investigator Assessment for Patients With Myelodysplastic Syndromes (MDS)
Timepoint [4] 0 0
3.5 years
Secondary outcome [5] 0 0
Maximum Plasma Concentration of Panobinostat After the First Dose in Arms 1 and 2
Timepoint [5] 0 0
Day 1
Secondary outcome [6] 0 0
Half Life of Panobinostat After the First Dose in Arms 1 and 2
Timepoint [6] 0 0
Day 1
Secondary outcome [7] 0 0
Maximum Plasma Concentration of Panobinostat After Multiple Doses in Arm 1 on Day 15
Timepoint [7] 0 0
Day 15
Secondary outcome [8] 0 0
Half Life of Panobinostat After Multiple Doses in Arm 1 on Day 15
Timepoint [8] 0 0
Day 15
Secondary outcome [9] 0 0
Geometric Mean Ratio (GMR) Comparing Treatment Days in Arm 1
Timepoint [9] 0 0
Day 15/day 1
Secondary outcome [10] 0 0
Percentages of Participants With Histone Acetylation Induction in Peripheral Blood in Arm 1 (MWF Every Week), Group X
Timepoint [10] 0 0
Days 1, 5, 8, 10, 15
Secondary outcome [11] 0 0
Percentages of Participants With Histone Acetylation Induction in Peripheral Blood in Arm 1 (MWF Every Week), Group Y
Timepoint [11] 0 0
Days 5, 8, end of study (up to 3.5 years)
Secondary outcome [12] 0 0
Percentages of Participants With Histone Acetylation Induction in Peripheral Blood in Arm 2 (MWF Every Other Week), Group X
Timepoint [12] 0 0
Days 5, 8, 10, 12, 15, End of study, Unscheduled (up to 3.5 years)
Secondary outcome [13] 0 0
Percentage of Participants With Histone Acetylation Induction in Peripheral Blood in Arm 2 (MWF Every Other Week), Group Y
Timepoint [13] 0 0
Days 5, 8, 10, 12, 15, End of study (up to 3.5 years)
Secondary outcome [14] 0 0
Highest Percent Change in Fetal Hemoglobin From Baseline in Arm 1 (MWF Every Week)
Timepoint [14] 0 0
Post dose to pre-dose (up to 3.5 years)
Secondary outcome [15] 0 0
Highest Percent Change of Fetal Hemoglobin From Baseline in Arm 2 (MWF Every Other Week)
Timepoint [15] 0 0
Post dose to pre-dose (up to 3.5 years)

Eligibility
Key inclusion criteria
Inclusion criteria:

* Adult patients (=18 years old) with advanced hematological malignancies who relapsed after or are refractory to standard therapy, or for which no standard therapy existed; or, were considered inappropriate candidates for standard therapy
* World Health Organization (WHO) performance status = 2
* Patients who met protocol-specified hematologic and non-hematologic laboratory values
* Patients with adequate liver and renal function
Minimum age
18 Years
Maximum age
No limit
Sex
Both males and females
Can healthy volunteers participate?
No
Key exclusion criteria
Exclusion criteria:

* Concurrent brain metastases or leukemic infiltration of the cerebrospinal fluid
* Peripheral neuropathy = CTCAE grade 2
* Unresolved diarrhea = CTCAE grade 2
* Concurrent severe and/or uncontrolled medical conditions which could compromise participation in the study, including impaired heart function or clinically significant heart disease, and impaired gastrointestinal function or disease that significantly altered aborption of LBH589
* Female patients who were pregnant or breast feeding
* Patients who were unwilling to use an effective method of birth control
* Patients who took medications specified by the protocol as prohibited for administration in combination with LBH589
* Patients with another primary malignancy that required active intervention or were clinically significant

Study design
Purpose of the study
Treatment
Allocation to intervention
Non-randomised trial
Procedure for enrolling a subject and allocating the treatment (allocation concealment procedures)
Methods used to generate the sequence in which subjects will be randomised (sequence generation)
Masking / blinding
Open (masking not used)
Who is / are masked / blinded?



Intervention assignment
Single group
Other design features
Phase
Phase 1
Type of endpoint/s
Statistical methods / analysis

Recruitment
Recruitment status
Completed
Data analysis
Reason for early stopping/withdrawal
Other reasons
Date of first participant enrolment
Anticipated
Actual
Date of last participant enrolment
Anticipated
Actual
Date of last data collection
Anticipated
Actual
Sample size
Target
Accrual to date
Final
Recruitment in Australia
Recruitment state(s)
VIC
Recruitment hospital [1] 0 0
Novartis Investigative Site - Parkville
Recruitment hospital [2] 0 0
Novartis Investigative Site - Prahran
Recruitment postcode(s) [1] 0 0
3002 - Parkville
Recruitment postcode(s) [2] 0 0
3181 - Prahran
Recruitment outside Australia
Country [1] 0 0
United States of America
State/province [1] 0 0
Georgia
Country [2] 0 0
United States of America
State/province [2] 0 0
Massachusetts
Country [3] 0 0
United States of America
State/province [3] 0 0
Texas
Country [4] 0 0
Germany
State/province [4] 0 0
Frankfurt/M
Country [5] 0 0
Germany
State/province [5] 0 0
Mainz

Funding & Sponsors
Primary sponsor type
Commercial sector/industry
Name
Novartis Pharmaceuticals
Address
Country

Ethics approval
Ethics application status

Summary
Brief summary
Trial website
Trial related presentations / publications
Public notes

Contacts
Principal investigator
Name 0 0
Novartis Pharmaceuticals
Address 0 0
Novartis Pharmaceuticals
Country 0 0
Phone 0 0
Fax 0 0
Email 0 0
Contact person for public queries
Name 0 0
Address 0 0
Country 0 0
Phone 0 0
Fax 0 0
Email 0 0
Contact person for scientific queries

No information has been provided regarding IPD availability


What supporting documents are/will be available?

No Supporting Document Provided



Results publications and other study-related documents

No documents have been uploaded by study researchers.