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Trial details imported from ClinicalTrials.gov

For full trial details, please see the original record at https://clinicaltrials.gov/study/NCT04401748




Registration number
NCT04401748
Ethics application status
Date submitted
22/05/2020
Date registered
26/05/2020

Titles & IDs
Public title
Study Of Venetoclax Tablet With Intravenous or Subcutaneous Azacitidine to Assess Change in Disease Activity In Adult Participants With Newly Diagnosed Higher-Risk Myelodysplastic Syndrome
Scientific title
A Randomized, Double-Blind, Phase 3 Study Evaluating the Safety and Efficacy of Venetoclax in Combination With Azacitidine in Patients Newly Diagnosed With Higher-Risk Myelodysplastic Syndrome (Higher-Risk MDS)
Secondary ID [1] 0 0
2023-507153-16-00
Secondary ID [2] 0 0
M15-954
Universal Trial Number (UTN)
Trial acronym
Verona
Linked study record

Health condition
Health condition(s) or problem(s) studied:
Myelodysplastic Syndrome (MDS) 0 0
Condition category
Condition code
Blood 0 0 0 0
Haematological diseases
Blood 0 0 0 0
Other blood disorders
Other 0 0 0 0
Research that is not of generic health relevance and not applicable to specific health categories listed above

Intervention/exposure
Study type
Interventional
Description of intervention(s) / exposure
Treatment: Drugs - Venetoclax
Treatment: Drugs - Azacitidine
Treatment: Drugs - Placebo

Experimental: Arm 1: Venetoclax + Azacitidine (AZA) - Participants will receive venetoclax once daily (QD) (Days 1-14) in combination with AZA QD (7 days of the first 9 days) of each 28 day cycle.

Active comparator: Arm 2: Placebo + Azacitidine - Participants will receive placebo once daily (QD) (Days 1-14) in combination with AZA QD (7 days of the first 9 days) of each 28 day cycle.


Treatment: Drugs: Venetoclax
Tablet: Oral

Treatment: Drugs: Azacitidine
Subcutaneous (SC) or Intravenous (IV) injection

Treatment: Drugs: Placebo
Tablet; Oral

Intervention code [1] 0 0
Treatment: Drugs
Comparator / control treatment
Control group

Outcomes
Primary outcome [1] 0 0
Overall survival (OS)
Timepoint [1] 0 0
Up To 5 Years
Secondary outcome [1] 0 0
Modified Overall Response (mOR)
Timepoint [1] 0 0
Up To 5 Years
Secondary outcome [2] 0 0
Percentage of Participants Achieving Overall Hematological Improvement (HI)
Timepoint [2] 0 0
Up to 5 Years
Secondary outcome [3] 0 0
Complete Remission (CR)
Timepoint [3] 0 0
Up To 36 Months
Secondary outcome [4] 0 0
Percentage of Participants Achieving Transfusion Independence (TI) Who are Transfusion Dependent at Baseline
Timepoint [4] 0 0
Up To 5 Years
Secondary outcome [5] 0 0
Time to Deterioration in Physical Functioning as Measured by Physical Functioning Domain of the European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire (EORTC QLQ-C30) Scale
Timepoint [5] 0 0
Up To 5 Years
Secondary outcome [6] 0 0
Change in Patient-Reported Outcomes Measurement Information System (PROMIS)-Fatigue Short Form (SF) 7a Scale Score
Timepoint [6] 0 0
Up To 5 Years
Secondary outcome [7] 0 0
Overall Response (OR)
Timepoint [7] 0 0
Up To 5 Years

Eligibility
Key inclusion criteria
* Participants with a diagnosis of Myelodysplastic Syndrome (MDS) according to the 2016 World Health Organization (WHO) classification wtih presence of < 20% bone marrow blasts per marrow biopsy/aspirate at screening.
* Participants must meet the following disease activity criteria:

* Overall Revised International Prognostic Scoring System (IPSS-R) score > 3 (intermediate, high or very high).
* Eastern Cooperative Oncology Group (ECOG) performance status of <= 2.
* Hematopoietic stem cell transplant (HSCT) eligible with no pre-arranged HSCT at the time of Study Day 1, or HSCT ineligible without plan for HSCT at the time of Study Day 1.
Minimum age
18 Years
Maximum age
No limit
Sex
Both males and females
Can healthy volunteers participate?
No
Key exclusion criteria
* Prior therapy for MDS with any hypomethylating agent, chemotherapy, or allogenic stem cell transplantation.
* Prior diagnosis of therapy-related MDS (t-MDS), MDS evolving from a pre-existing myeloproliferative neoplasm (MPN), MDS/MPN including chronic myelomonocytic leukemia (CMML), atypical chronic myeloid leukemia (aCML), juvenile myelomonocytic leukemia (JMML) and unclassifiable MDS/MPN.

Study design
Purpose of the study
Treatment
Allocation to intervention
Randomised controlled trial
Procedure for enrolling a subject and allocating the treatment (allocation concealment procedures)
Methods used to generate the sequence in which subjects will be randomised (sequence generation)
Masking / blinding
Blinded (masking used)
Who is / are masked / blinded?
The people receiving the treatment/s
The people administering the treatment/s
The people assessing the outcomes
The people analysing the results/data
Intervention assignment
Parallel
Other design features
Phase
Phase 3
Type of endpoint/s
Statistical methods / analysis

Recruitment
Recruitment status
Active, not recruiting
Data analysis
Reason for early stopping/withdrawal
Other reasons
Date of first participant enrolment
Anticipated
Actual
Date of last participant enrolment
Anticipated
Actual
Date of last data collection
Anticipated
Actual
Sample size
Target
Accrual to date
Final
Recruitment in Australia
Recruitment state(s)
NSW,QLD,SA,VIC
Recruitment hospital [1] 0 0
Duplicate_Blacktown Hospital /ID# 234079 - Blacktown
Recruitment hospital [2] 0 0
St George Hospital /ID# 221810 - Kogarah
Recruitment hospital [3] 0 0
Port Macquarie Base Hospital /ID# 234078 - Port Macquarie
Recruitment hospital [4] 0 0
Gold coast University Hospital /ID# 222606 - SouthPort
Recruitment hospital [5] 0 0
Royal Adelaide Hospital /ID# 221805 - Adelaide
Recruitment hospital [6] 0 0
St Vincent's Hospital Melbourne /ID# 221809 - Fitzroy Melbourne
Recruitment hospital [7] 0 0
Austin Health /ID# 221807 - Heidelberg
Recruitment postcode(s) [1] 0 0
2148 - Blacktown
Recruitment postcode(s) [2] 0 0
2217 - Kogarah
Recruitment postcode(s) [3] 0 0
2444 - Port Macquarie
Recruitment postcode(s) [4] 0 0
4215 - SouthPort
Recruitment postcode(s) [5] 0 0
5000 - Adelaide
Recruitment postcode(s) [6] 0 0
3065 - Fitzroy Melbourne
Recruitment postcode(s) [7] 0 0
3084 - Heidelberg
Recruitment outside Australia
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Ankara
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Samsun
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Tuzla
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Bristol, City Of
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Devon
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Dorset
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Oxfordshire
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Wales
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Aberdeen
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Birmingham
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London

Funding & Sponsors
Primary sponsor type
Commercial sector/industry
Name
AbbVie
Address
Country
Other collaborator category [1] 0 0
Commercial sector/industry
Name [1] 0 0
Genentech, Inc.
Address [1] 0 0
Country [1] 0 0

Ethics approval
Ethics application status

Summary
Brief summary
Trial website
Trial related presentations / publications
Public notes

Contacts
Principal investigator
Name 0 0
ABBVIE INC.
Address 0 0
AbbVie
Country 0 0
Phone 0 0
Fax 0 0
Email 0 0
Contact person for public queries
Name 0 0
Address 0 0
Country 0 0
Phone 0 0
Fax 0 0
Email 0 0
Contact person for scientific queries

Data sharing statement
Will individual participant data (IPD) for this trial be available (including data dictionaries)?
Yes
What data in particular will be shared?
AbbVie is committed to responsible data sharing regarding the clinical trials we sponsor. This includes access to anonymized, individual and trial-level data (analysis data sets), as well as other information (e.g., protocols, analyses plans, clinical study reports), as long as the trials are not part of an ongoing or planned regulatory submission. This includes requests for clinical trial data for unlicensed products and indications.

Supporting document/s available: Study protocol, Statistical analysis plan (SAP), Clinical study report (CSR)
When will data be available (start and end dates)?
For details on when studies are available for sharing visit https://vivli.org/ourmember/abbvie/
Available to whom?
Access to this clinical trial data can be requested by any qualified researchers who engage in rigorous independent scientific research, and will be provided following review and approval of a research proposal and statistical analysis plan and execution of a data sharing statement. Data requests can be submitted at any time after approval in the US and/or EU and a primary manuscript is accepted for publication. For more information on the process, or to submit a request, visit the following link https://www.abbvieclinicaltrials.com/hcp/data-sharing/
Available for what types of analyses?
How or where can data be obtained?
IPD available at link: https://vivli.org/ourmember/abbvie/


What supporting documents are/will be available?

No Supporting Document Provided



Results publications and other study-related documents

No documents have been uploaded by study researchers.