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Trial details imported from ClinicalTrials.gov

For full trial details, please see the original record at https://clinicaltrials.gov/study/NCT05349643




Registration number
NCT05349643
Ethics application status
Date submitted
22/04/2022
Date registered
27/04/2022

Titles & IDs
Public title
A Study to Evaluate Safety and Efficacy of AMB-05X Injections in Subjects With TGCT
Scientific title
A Phase 2, Open-Label, Adaptive, Dose-Ranging Study With Long-Term Extension to Evaluate the Safety, Tolerability, Efficacy, and Pharmacokinetics of Intra Articular AMB-05X Injections in Subjects With Tenosynovial Giant Cell Tumor
Secondary ID [1] 0 0
AMB-051-07
Universal Trial Number (UTN)
Trial acronym
Linked study record

Health condition
Health condition(s) or problem(s) studied:
Pigmented Villonodular Synovitis 0 0
TGCT 0 0
Tenosynovial Giant Cell Tumor 0 0
Condition category
Condition code
Cancer 0 0 0 0
Bone
Cancer 0 0 0 0
Other cancer types
Musculoskeletal 0 0 0 0
Other muscular and skeletal disorders

Intervention/exposure
Study type
Interventional
Description of intervention(s) / exposure
Treatment: Other - AMB-05X

Experimental: AMB-05X - Subjects will receive an injection of AMB-05X once every 4 weeks for 24 weeks (for 6 treatments total). Based on ongoing review of the available safety, PK, PD, and efficacy data, the Sponsor may either increase or decrease the dose.


Treatment: Other: AMB-05X
A fully human monoclonal immunoglobulin (IgG2) directed against c-fms

Intervention code [1] 0 0
Treatment: Other
Comparator / control treatment
Control group

Outcomes
Primary outcome [1] 0 0
Objective Response Rate - Part 1
Timepoint [1] 0 0
Part 1 Week 24
Primary outcome [2] 0 0
Treatment-emergent adverse events
Timepoint [2] 0 0
Part 1 Week 24 and Part 2 Week 72
Secondary outcome [1] 0 0
Objective Response Rate
Timepoint [1] 0 0
Part 2 Week 72
Secondary outcome [2] 0 0
Objective Response Rate (AMB-051-01 subjects)
Timepoint [2] 0 0
Part 2 Week 72
Secondary outcome [3] 0 0
Objective Response Rate (ORR) per modified Response Evaluation Criteria in Solid Tumors Version 1.1
Timepoint [3] 0 0
Part 1 Week 24
Secondary outcome [4] 0 0
Objective Response Rate (ORR) per modified Response Evaluation Criteria in Solid Tumors Version 1.1
Timepoint [4] 0 0
Part 2 Week 72
Secondary outcome [5] 0 0
Tumor response based on tumor volume score (TVS)
Timepoint [5] 0 0
Part 1 Week 24
Secondary outcome [6] 0 0
Tumor response based on tumor volume score (TVS)
Timepoint [6] 0 0
Part 2 Week 72
Secondary outcome [7] 0 0
Duration of Response by Response Evaluation Criteria in Solid Tumors
Timepoint [7] 0 0
Part 1 Week 24
Secondary outcome [8] 0 0
Duration of Response by Response Evaluation Criteria in Solid Tumors v1.1
Timepoint [8] 0 0
Part 2 Week 72
Secondary outcome [9] 0 0
Duration of Response by Modified Response Evaluation Criteria in Solid Tumors
Timepoint [9] 0 0
Part 1 Week 24
Secondary outcome [10] 0 0
Duration of Response by Modified Response Evaluation Criteria in Solid Tumors
Timepoint [10] 0 0
Part 2 Week 72
Secondary outcome [11] 0 0
Duration of Response by tumor volume score
Timepoint [11] 0 0
Part 1 Week 24
Secondary outcome [12] 0 0
Duration of Response by tumor volume score
Timepoint [12] 0 0
Part 2 Week 72
Secondary outcome [13] 0 0
Time to Response by Response Evaluation Criteria in Solid Tumors
Timepoint [13] 0 0
Part 1 Week 24
Secondary outcome [14] 0 0
Time to Response by Response Evaluation Criteria in Solid Tumors
Timepoint [14] 0 0
Part 2 Week 72
Secondary outcome [15] 0 0
Time to Response by Modified Response Evaluation Criteria in Solid Tumors
Timepoint [15] 0 0
Part 1 week 24
Secondary outcome [16] 0 0
Time to Response by Modified Response Evaluation Criteria in Solid Tumors
Timepoint [16] 0 0
Part 2 Week 72
Secondary outcome [17] 0 0
Time to Response per tumor volume score
Timepoint [17] 0 0
Part 1 Week 24
Secondary outcome [18] 0 0
Time to Response per tumor volume score
Timepoint [18] 0 0
Part 2 Week 72
Secondary outcome [19] 0 0
Mean change from Baseline in joint range of motion (ROM)
Timepoint [19] 0 0
Part 1 Week 24
Secondary outcome [20] 0 0
Mean change from Baseline in joint range of motion (ROM)
Timepoint [20] 0 0
Part 2 Week 72
Secondary outcome [21] 0 0
Mean change from Baseline in the Patient-Reported Outcomes Measurement Information System (PROMIS) Physical Function score
Timepoint [21] 0 0
Part 1 Week 24
Secondary outcome [22] 0 0
Mean change from Baseline in the Patient-Reported Outcomes Measurement Information System (PROMIS) Physical Function score
Timepoint [22] 0 0
Part 2 Week 72
Secondary outcome [23] 0 0
Mean change from Baseline in Worst Stiffness Numeric Rating Scale score
Timepoint [23] 0 0
Part 1 Week 24
Secondary outcome [24] 0 0
Mean change from Baseline in Worst Stiffness Numeric Rating Scale score
Timepoint [24] 0 0
Part 2 Week 72
Secondary outcome [25] 0 0
Mean change from Baseline in the Brief Pain Inventory (BPI) score
Timepoint [25] 0 0
Part 1 Week 24
Secondary outcome [26] 0 0
Mean change from Baseline in the Brief Pain Inventory (BPI) score
Timepoint [26] 0 0
Part 2 Week 72
Secondary outcome [27] 0 0
Decrease of at least 30% in mean Brief Pain Inventory (BPI) from Baseline
Timepoint [27] 0 0
Part 1 Week 24
Secondary outcome [28] 0 0
Decrease of at least 30% in mean Brief Pain Inventory (BPI) from Baseline
Timepoint [28] 0 0
Part 2 Week 72
Secondary outcome [29] 0 0
Mean change from Baseline in Patient-Reported Outcomes Measurement Information System Pain Interference score
Timepoint [29] 0 0
Part 1 Week 24
Secondary outcome [30] 0 0
Mean change from Baseline in Patient-Reported Outcomes Measurement Information System Pain Interference score
Timepoint [30] 0 0
Part 2 Week 72
Secondary outcome [31] 0 0
Mean change from Baseline in Patient Global Impression of Change in Physical Functioning for capacity to perform everyday tasks
Timepoint [31] 0 0
Part 1 Week 24
Secondary outcome [32] 0 0
Mean change from Baseline in Patient Global Impression of Change in Physical Functioning for capacity to perform everyday tasks
Timepoint [32] 0 0
Part 2 Week 72
Secondary outcome [33] 0 0
Mean change from Baseline in Patient Global Impression of Change in tenosynovial giant cell tumor-related stiffness score
Timepoint [33] 0 0
Part 1 Week 24
Secondary outcome [34] 0 0
Mean change from Baseline in Patient Global Impression of Change in tenosynovial giant cell tumor-related stiffness score
Timepoint [34] 0 0
Part 2 Week 72
Secondary outcome [35] 0 0
Mean change from Baseline in Worst Pain Numeric Rating Scale score
Timepoint [35] 0 0
Part 1 Week 24
Secondary outcome [36] 0 0
Mean change from Baseline in Worst Pain Numeric Rating Scale score
Timepoint [36] 0 0
Part 2 Week 72
Secondary outcome [37] 0 0
EuroQol 5 Dimension 5 Level Health Assessment
Timepoint [37] 0 0
Part 1 Week 24
Secondary outcome [38] 0 0
EuroQol 5 Dimension 5 Level Health Assessment
Timepoint [38] 0 0
Part 2 Week 72

Eligibility
Key inclusion criteria
1. Subject = 18 years
2. TGCT with only 1 joint involvement
3. Symptomatic Measurable disease of at least 1 cm based on RECIST v1.1
4. Stable prescription of analgesic regimen
5. Agrees to follow contraception guidelines
6. Women of childbearing potential must have a negative pregnancy test
7. Adequate hematologic, hepatic, and renal function
Minimum age
18 Years
Maximum age
No limit
Sex
Both males and females
Can healthy volunteers participate?
No
Key exclusion criteria
1. Prior investigational drug use within 4 weeks or 5 half-lives of Baseline
2. Previous use of therapeutics targeting CSF1 or CSF1R or oral tyrosine kinase inhibitors within 3 months prior to Baseline
3. History of extensive or reconstructive surgery on the affected joint
4. Active cancer (either currently or within 3 mo before Baseline) that requires/required therapy (e.g., surgery, chemotherapy, or radiation therapy)
5. Metastatic or malignant transformation of TGCT
6. Hepatitis C virus (HCV) or hepatitis B virus (HBV) or human immunodeficiency virus (HIV)
7. Known active tuberculosis
8. Significant concomitant arthropathy in the affected joint, serious illness, uncontrolled infection, or a medical or psychiatric history
9. Women who are breastfeeding
10. A screening Fridericia-corrected QT interval (QTcF) = 470 ms
11. MRI contraindications (e.g., pacemaker, loose metallic implants)
12. History of hypersensitivity to any ingredient of the study drug
13. History of drug or alcohol abuse within 3 months before baseline
14. Any other severe acute or chronic medical or psychiatric condition or clinically significant laboratory abnormality that may increase the risk associated with study participation/treatment or interfere with interpretation of study results and, in the Investigator's opinion, make the subject inappropriate for this study
15. Subjects who, in the Investigator's opinion, should not participate in the study for any reason, including if there is a question about their ability to comply with study requirements

Study design
Purpose of the study
Treatment
Allocation to intervention
NA
Procedure for enrolling a subject and allocating the treatment (allocation concealment procedures)
Methods used to generate the sequence in which subjects will be randomised (sequence generation)
Masking / blinding
Open (masking not used)
Who is / are masked / blinded?



Intervention assignment
Single group
Other design features
Phase
Phase 2
Type of endpoint/s
Statistical methods / analysis

Recruitment
Recruitment status
Completed
Data analysis
Reason for early stopping/withdrawal
Other reasons
Date of first participant enrolment
Anticipated
Actual
Date of last participant enrolment
Anticipated
Actual
Date of last data collection
Anticipated
Actual
Sample size
Target
Accrual to date
Final
Recruitment in Australia
Recruitment state(s)
Recruitment hospital [1] 0 0
AmMax Bio, Clinical Site - Camperdown
Recruitment hospital [2] 0 0
AmMax Bio, Clinical Site - Woolloongabba
Recruitment postcode(s) [1] 0 0
- Camperdown
Recruitment postcode(s) [2] 0 0
- Woolloongabba
Recruitment outside Australia
Country [1] 0 0
United States of America
State/province [1] 0 0
California
Country [2] 0 0
United States of America
State/province [2] 0 0
Florida
Country [3] 0 0
United States of America
State/province [3] 0 0
Texas
Country [4] 0 0
Netherlands
State/province [4] 0 0
Leiden

Funding & Sponsors
Primary sponsor type
Commercial sector/industry
Name
AmMax Bio, Inc.
Address
Country

Ethics approval
Ethics application status

Summary
Brief summary
Trial website
Trial related presentations / publications
Public notes

Contacts
Principal investigator
Name 0 0
Dorothy Nguyen, MD
Address 0 0
AmMax Bio
Country 0 0
Phone 0 0
Fax 0 0
Email 0 0
Contact person for public queries
Name 0 0
Tiffany Nguyen
Address 0 0
Country 0 0
Phone 0 0
6502856560
Fax 0 0
Email 0 0
Contact person for scientific queries

Data sharing statement
Will individual participant data (IPD) for this trial be available (including data dictionaries)?
No
No/undecided IPD sharing reason/comment


What supporting documents are/will be available?

No Supporting Document Provided



Results publications and other study-related documents

No documents have been uploaded by study researchers.