The ANZCTR website will be unavailable from 1pm until 3pm (AEDT) on Wednesday the 30th of October for website maintenance. Please be sure to log out of the system in order to avoid any loss of data.

The safety and scientific validity of this study is the responsibility of the study sponsor and investigators. Listing a study does not mean it has been endorsed by the ANZCTR. Before participating in a study, talk to your health care provider and refer to this information for consumers
Trial details imported from ClinicalTrials.gov

For full trial details, please see the original record at https://clinicaltrials.gov/study/NCT02200770




Registration number
NCT02200770
Ethics application status
Date submitted
16/07/2014
Date registered
25/07/2014

Titles & IDs
Public title
N-MOmentum: A Clinical Research Study of Inebilizumab in Neuromyelitis Optica Spectrum Disorders
Scientific title
A Double-masked, Placebo-controlled Study With Open-label Period to Evaluate the Efficacy and Safety of MEDI-551 in Adult Subjects With Neuromyelitis Optica and Neuromyelitis Optica Spectrum Disorders.
Secondary ID [1] 0 0
2014-000253-36
Secondary ID [2] 0 0
CD-IA-MEDI-551-1155
Universal Trial Number (UTN)
Trial acronym
Linked study record

Health condition
Health condition(s) or problem(s) studied:
Neuromyelitis Optica and Neuromyelitis Optica Spectrum Disorders 0 0
Condition category
Condition code
Inflammatory and Immune System 0 0 0 0
Autoimmune diseases
Neurological 0 0 0 0
Other neurological disorders
Eye 0 0 0 0
Diseases / disorders of the eye

Intervention/exposure
Study type
Interventional
Description of intervention(s) / exposure
Treatment: Drugs - Inebilizumab
Other interventions - Placebo

Placebo comparator: Placebo/Inebilizumab - Aquaporin-4-antibody (AQP4-IgG) sero positive and sero negative participants will receive IV dose of placebo matched to inebilizumab on Day 1 and Day 15 of the RCP. The participants who enter OLP will receive IV inebilizumab 300 mg on both Day 1 and Day 15, followed by a single IV dose of inebilizumab 300 mg every 6 months until maximum of 3 years after the last participant enters the OLP. Participants will have choice to enter in the SFP at any point during RCP or OLP and will be free to pursue other treatment options otherwise prohibited during the RCP and OLP. Participants will continue in the SFP for 12 months from last dose of study drug.

Experimental: Inebilizumab/Inebilizumab - AQP4-IgG sero positive and sero negative participants will IV dose of inebilizumab 300 mg on Day 1 and Day 15 of RCP. The participants who enter OLP will receive IV inebilizumab 300 mg on Day 1 and matching placebo on Day 15, followed by a single IV dose of inebilizumab 300 mg every 6 months until maximum of 3 years after the last participant enters the OLP. Participants will have choice to enter in the SFP at any point during RCP or OLP and will be free to pursue other treatment options otherwise prohibited during the RCP and OLP. Participants will continue in the SFP for 12 months from last dose of study drug.


Treatment: Drugs: Inebilizumab
Participants will receive IV inebilizumab 300 mg.

Other interventions: Placebo
Participants will receive IV placebo matched to inebilizumab.

Intervention code [1] 0 0
Treatment: Drugs
Intervention code [2] 0 0
Other interventions
Comparator / control treatment
Control group

Outcomes
Primary outcome [1] 0 0
Time to Adjudication Committee (AC)-Determined Neuromyelitis Optica Spectrum Disorder (NMOSD) Attack During RCP
Timepoint [1] 0 0
Day 1 (Baseline) through Day 197
Secondary outcome [1] 0 0
Percentage of Participants With Worsening in Expanded Disability Severity Scale (EDSS) Score From Baseline to the Last Visit of RCP
Timepoint [1] 0 0
Day 1 (Baseline) through Day 197
Secondary outcome [2] 0 0
Change From Baseline in Low-Contrast Visual Acuity Binocular Score to the Last Visit of RCP
Timepoint [2] 0 0
Day 1 (Baseline) through Day 197
Secondary outcome [3] 0 0
Cumulative Number of Active Magnetic Resonance Imaging (MRI) Lesions During RCP
Timepoint [3] 0 0
From Screening (Day -28) to Day 197
Secondary outcome [4] 0 0
Number of NMOSD-related In-patient Hospitalizations During RCP
Timepoint [4] 0 0
Day 1 (Baseline) through Day 197
Secondary outcome [5] 0 0
Annualized AC-determined NMOSD Attack Rate During Any Exposure to Inebilizumab
Timepoint [5] 0 0
For participants randomized to inebilizumab: Day 1 of RCP through end of OLP (approximately 3.5 years); and for participants randomized to placebo: Day 1 of OLP through the end of OLP (approximately 3 years)
Secondary outcome [6] 0 0
Number of Participants With Treatment Emergent Adverse Events (TEAEs) and Treatment Emergent Serious Adverse Events (TESAEs) During RCP
Timepoint [6] 0 0
Day 1 (Baseline) through Day 197
Secondary outcome [7] 0 0
Number of Participants With TEAEs and TESAEs During OLP
Timepoint [7] 0 0
Day 198 through end of OLP period (maximum of 3 years after the last participant entered, until regulatory approval or study discontinuation, whichever occurs first) (approximately 3 years)
Secondary outcome [8] 0 0
Number of Participants With TEAEs and TESAEs During SFP (Open-label Population)
Timepoint [8] 0 0
Every 3 months for a total of 1 year after the last dose of study drug (approximately 3 years)
Secondary outcome [9] 0 0
Number of Participants With TEAEs and TESAEs During SFP (Non-OLP Population)
Timepoint [9] 0 0
Every 3 months for a total of 1 year after the last dose of study drug (approximately 3 years)
Secondary outcome [10] 0 0
Number of Participants With at Least a 2-Grade Shift From Baseline to Worst Toxicity Grade in Hematology and Chemistry During RCP
Timepoint [10] 0 0
Day 1 (Baseline) through Day 197
Secondary outcome [11] 0 0
Number of Participants With at Least a 2-Grade Shift From Baseline to Worst Toxicity Grade in Hematology and Chemistry During OLP
Timepoint [11] 0 0
Day 198 through end of OLP (maximum of 3 years after the last participant enters, until regulatory approval or study discontinuation, whichever occurs first) (approximately 3 years)
Secondary outcome [12] 0 0
Time to Maximum Serum Concentration (Tmax) of Inebilizumab (During RCP)
Timepoint [12] 0 0
Dose 1 (Pre and post dose on Day 1 and Day 8); and Dose 2 (pre and post dose on Day 15; and Days 29, 57, 85, 113, 155, and 197)
Secondary outcome [13] 0 0
Maximum Observed Serum Concentration (Cmax) of Inebilizumab (During RCP)
Timepoint [13] 0 0
Dose 1 (Pre and post dose on Day 1 and Day 8); and Dose 2 (pre and post dose on Day 15; and Days 29, 57, 85, 113, 155, and 197)
Secondary outcome [14] 0 0
Area Under the Serum Concentration Time Curve of the Dosing Interval (AUC0-14d) of Inebilizumab (During RCP)
Timepoint [14] 0 0
Dose 1 (Pre and post dose on Day 1 and Day 8); and Dose 2 (pre and post dose on Day 15; and Days 29, 57, 85, 113, 155, and 197)
Secondary outcome [15] 0 0
Number of Participants With Positive Anti-Drug Antibodies (ADA) Titer to Inebilizumab (During RCP)
Timepoint [15] 0 0
Pre and post dose on Day 1; and on Days 29, 85, and 197
Secondary outcome [16] 0 0
Number of Participants With Positive Anti-Drug Antibodies (ADA) Titer to Inebilizumab (During OLP)
Timepoint [16] 0 0
Pre and post dose on Day 1; and on Days 92, 183, 274, and then every 6 months (maximum of 3 years after the last participant enters, until regulatory approval or study discontinuation, whichever occurs first) (approximately 3 years)

Eligibility
Key inclusion criteria
1. Men and women 18 years or older with diagnosis of NMO/NMOSD
2. Confirmation of NMO/NMOSD status:

1. AQP4-IgG sero-positive NMO/NMOSD with at least one attack requiring rescue therapy in the last year or two attacks requiring rescue therapy in the last 2 years
2. AQP4-IgG sero-negative NMO with at least one attack requiring rescue therapy in the last year or two attacks requiring rescue therapy in the last 2 years
3. Able and willing to give written informed consent and comply with the requirements of the study protocol.
4. EDSS <= 7.5 (8 in special circumstances)
5. Men and women of reproductive potential must agree to use a highly effective method of birth control from screening to 6 months after final dose of the investigational product.
Minimum age
18 Years
Maximum age
No limit
Sex
Both males and females
Can healthy volunteers participate?
No
Key exclusion criteria
1. Lactating and pregnant females
2. Treatment with any investigational agent within 4 weeks of screening
3. Known history of a severe allergy or reaction to any component of the investigational product formulation or history of anaphylaxis following any biologic therapy.
4. Known active severe bacterial, viral, or other infection or any major episode of infection requiring hospitalization.
5. History of alcohol, drug, or chemical abuse, or a recent history of such abuse < 1 year prior to randomization
6. Receipt of the following at any time prior to randomization:

1. Alemtuzumab
2. Total lymphoid irradiation
3. Bone marrow transplant
4. T-cell vaccination therapy
7. Receipt of rituximab or any experimental B-cell depleting agent within 6 months prior screening and B-cells below the lower limit of normal.
8. Receipt of intravenous immunoglobulin (IVIG) within 1 month prior to randomization.
9. Receipt of any of the following within 3 months prior to randomization:

1. Natalizumab (Tysabri®).
2. Cyclosporin
3. Methotrexate
4. Mitoxantrone
5. Cyclophosphamide
6. Tocilizumab
7. Eculizumab
10. History of Hepatitis B and/or Hepatitis C (Hep B/C at screening)
11. Known history of a primary immunodeficiency (congenital or acquired) or an underlying condition such as human immunodeficiency virus (HIV) infection
12. History of malignancies, apart from squamous cell or basal cell carcinoma of the skin treated with documented success of curative therapy > 3 months prior to randomization
13. Any concomitant disease other than NMO/NMOSD that required treatment with oral or intravenous steroids at doses over 20 mg a day for over 21 days

Study design
Purpose of the study
Treatment
Allocation to intervention
Randomised controlled trial
Procedure for enrolling a subject and allocating the treatment (allocation concealment procedures)
Methods used to generate the sequence in which subjects will be randomised (sequence generation)
Masking / blinding
Blinded (masking used)
Who is / are masked / blinded?
The people receiving the treatment/s
The people administering the treatment/s
The people assessing the outcomes
The people analysing the results/data
Intervention assignment
Parallel
Other design features
Phase
Phase 2
Type of endpoint/s
Statistical methods / analysis

Recruitment
Recruitment status
Completed
Data analysis
Reason for early stopping/withdrawal
Other reasons
Date of first participant enrolment
Anticipated
Actual
Date of last participant enrolment
Anticipated
Actual
Date of last data collection
Anticipated
Actual
Sample size
Target
Accrual to date
Final
Recruitment in Australia
Recruitment state(s)
Recruitment hospital [1] 0 0
Research Site - Melbourne
Recruitment postcode(s) [1] 0 0
3065 - Melbourne
Recruitment outside Australia
Country [1] 0 0
United States of America
State/province [1] 0 0
Alabama
Country [2] 0 0
United States of America
State/province [2] 0 0
California
Country [3] 0 0
United States of America
State/province [3] 0 0
Colorado
Country [4] 0 0
United States of America
State/province [4] 0 0
Connecticut
Country [5] 0 0
United States of America
State/province [5] 0 0
Florida
Country [6] 0 0
United States of America
State/province [6] 0 0
Illinois
Country [7] 0 0
United States of America
State/province [7] 0 0
Kansas
Country [8] 0 0
United States of America
State/province [8] 0 0
Maryland
Country [9] 0 0
United States of America
State/province [9] 0 0
Michigan
Country [10] 0 0
United States of America
State/province [10] 0 0
Minnesota
Country [11] 0 0
United States of America
State/province [11] 0 0
Missouri
Country [12] 0 0
United States of America
State/province [12] 0 0
North Carolina
Country [13] 0 0
United States of America
State/province [13] 0 0
Ohio
Country [14] 0 0
United States of America
State/province [14] 0 0
Texas
Country [15] 0 0
United States of America
State/province [15] 0 0
Virginia
Country [16] 0 0
Bulgaria
State/province [16] 0 0
Sofia
Country [17] 0 0
Bulgaria
State/province [17] 0 0
Varna
Country [18] 0 0
Canada
State/province [18] 0 0
British Columbia
Country [19] 0 0
Colombia
State/province [19] 0 0
Barranquilla
Country [20] 0 0
Colombia
State/province [20] 0 0
Bogota
Country [21] 0 0
Colombia
State/province [21] 0 0
Cali
Country [22] 0 0
Czechia
State/province [22] 0 0
Olomouc
Country [23] 0 0
Czechia
State/province [23] 0 0
Praha 2
Country [24] 0 0
Czechia
State/province [24] 0 0
Teplice
Country [25] 0 0
Estonia
State/province [25] 0 0
Tallinn
Country [26] 0 0
Estonia
State/province [26] 0 0
Tartu
Country [27] 0 0
Germany
State/province [27] 0 0
Berlin
Country [28] 0 0
Germany
State/province [28] 0 0
Dresden
Country [29] 0 0
Germany
State/province [29] 0 0
Düsseldorf
Country [30] 0 0
Germany
State/province [30] 0 0
Leipzig
Country [31] 0 0
Germany
State/province [31] 0 0
Muenster
Country [32] 0 0
Germany
State/province [32] 0 0
Rostock
Country [33] 0 0
Hong Kong
State/province [33] 0 0
HongKong
Country [34] 0 0
Hungary
State/province [34] 0 0
Esztergom
Country [35] 0 0
Hungary
State/province [35] 0 0
Nyíregyháza
Country [36] 0 0
Hungary
State/province [36] 0 0
Szeged
Country [37] 0 0
Israel
State/province [37] 0 0
Jerusalem
Country [38] 0 0
Israel
State/province [38] 0 0
Ramat Gan
Country [39] 0 0
Israel
State/province [39] 0 0
Tel Aviv
Country [40] 0 0
Japan
State/province [40] 0 0
Aomori-shi
Country [41] 0 0
Japan
State/province [41] 0 0
Bunkyo-ku
Country [42] 0 0
Japan
State/province [42] 0 0
Kyoto-shi
Country [43] 0 0
Japan
State/province [43] 0 0
Ota-ku
Country [44] 0 0
Japan
State/province [44] 0 0
Sendai-shi
Country [45] 0 0
Japan
State/province [45] 0 0
Tsukuba
Country [46] 0 0
Korea, Republic of
State/province [46] 0 0
Goyang
Country [47] 0 0
Korea, Republic of
State/province [47] 0 0
Jongno-gu
Country [48] 0 0
Korea, Republic of
State/province [48] 0 0
Seoul
Country [49] 0 0
Mexico
State/province [49] 0 0
Ciudad De Mexico
Country [50] 0 0
Mexico
State/province [50] 0 0
Mexico City
Country [51] 0 0
Mexico
State/province [51] 0 0
Monterrey
Country [52] 0 0
Mexico
State/province [52] 0 0
San Luis Potosi
Country [53] 0 0
Moldova, Republic of
State/province [53] 0 0
Chisinau
Country [54] 0 0
New Zealand
State/province [54] 0 0
Auckland
Country [55] 0 0
Peru
State/province [55] 0 0
Bellavista
Country [56] 0 0
Peru
State/province [56] 0 0
Lima
Country [57] 0 0
Poland
State/province [57] 0 0
Katowice
Country [58] 0 0
Poland
State/province [58] 0 0
Krakow
Country [59] 0 0
Poland
State/province [59] 0 0
Lublin
Country [60] 0 0
Poland
State/province [60] 0 0
Lódz
Country [61] 0 0
Poland
State/province [61] 0 0
Olsztyn
Country [62] 0 0
Poland
State/province [62] 0 0
Warszawa
Country [63] 0 0
Russian Federation
State/province [63] 0 0
Belgorod
Country [64] 0 0
Russian Federation
State/province [64] 0 0
Kazan
Country [65] 0 0
Russian Federation
State/province [65] 0 0
Khabarovsk
Country [66] 0 0
Russian Federation
State/province [66] 0 0
Krasnoyarsk
Country [67] 0 0
Russian Federation
State/province [67] 0 0
Moscow
Country [68] 0 0
Russian Federation
State/province [68] 0 0
Nizhniy Novgorod
Country [69] 0 0
Russian Federation
State/province [69] 0 0
Novosibirsk
Country [70] 0 0
Russian Federation
State/province [70] 0 0
Omsk
Country [71] 0 0
Russian Federation
State/province [71] 0 0
Saint-Petersburg
Country [72] 0 0
Russian Federation
State/province [72] 0 0
Ufa
Country [73] 0 0
Serbia
State/province [73] 0 0
Belgrade
Country [74] 0 0
South Africa
State/province [74] 0 0
Cape Town
Country [75] 0 0
Spain
State/province [75] 0 0
Madrid
Country [76] 0 0
Taiwan
State/province [76] 0 0
Changhua City
Country [77] 0 0
Taiwan
State/province [77] 0 0
Hualien City
Country [78] 0 0
Taiwan
State/province [78] 0 0
Tainan City
Country [79] 0 0
Thailand
State/province [79] 0 0
Bangkok
Country [80] 0 0
Thailand
State/province [80] 0 0
Muang
Country [81] 0 0
Turkey
State/province [81] 0 0
Istanbul
Country [82] 0 0
Turkey
State/province [82] 0 0
Izmir
Country [83] 0 0
Turkey
State/province [83] 0 0
Samsun

Funding & Sponsors
Primary sponsor type
Commercial sector/industry
Name
MedImmune LLC
Address
Country

Ethics approval
Ethics application status

Summary
Brief summary
Trial website
Trial related presentations / publications
Public notes

Contacts
Principal investigator
Name 0 0
MedImmune, LLC MedImmune, LLC
Address 0 0
MedImmune LLC
Country 0 0
Phone 0 0
Fax 0 0
Email 0 0
Contact person for public queries
Name 0 0
Address 0 0
Country 0 0
Phone 0 0
Fax 0 0
Email 0 0
Contact person for scientific queries

Data sharing statement
Will individual participant data (IPD) for this trial be available (including data dictionaries)?
Yes
What data in particular will be shared?
Qualified researchers can request access to anonymized individual patient-level data from AstraZeneca group of companies sponsored clinical trials via the request portal. All request will be evaluated as per the AZ disclosure commitment: https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.

Yes, indicates that AZ are accepting requests for IPD, but this does not mean all requests will be shared

Supporting document/s available: Study protocol, Statistical analysis plan (SAP)
When will data be available (start and end dates)?
AstraZeneca will meet or exceed data availability as per the commitments made to the EFPIA Pharma Data Sharing Principles. For details of our timelines, please rerefer to our disclosure commitment at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
Available to whom?
When a request has been approved AstraZeneca will provide access to the de-identified individual patient-level data in an approved sponsored tool. Signed Data Sharing Agreement (non-negotiable contract for data accessors) must be in place before accessing requested information. Additionally, all users will need to accept the terms and conditions of the SAS MSE to gain access. For additional details, please review the Disclosure Statements at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
Available for what types of analyses?
How or where can data be obtained?
IPD available at link: https://astrazenecagroup-dt.pharmacm.com/DT/Home


What supporting documents are/will be available?

Results publications and other study-related documents

No documents have been uploaded by study researchers.