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Trial details imported from ClinicalTrials.gov

For full trial details, please see the original record at https://clinicaltrials.gov/study/NCT02130557




Registration number
NCT02130557
Ethics application status
Date submitted
1/05/2014
Date registered
5/05/2014

Titles & IDs
Public title
A Multicenter Phase 3, Open-Label Study of Bosutinib Versus Imatinib in Adult Patients With Newly Diagnosed Chronic Phase Chronic Myelogenous Leukemia
Scientific title
A MULTICENTER PHASE 3 RANDOMIZED, OPEN-LABEL STUDY OF BOSUTINIB VERSUS IMATINIB IN ADULT PATIENTS WITH NEWLY DIAGNOSED CHRONIC PHASE CHRONIC MYELOGENOUS LEUKEMIA
Secondary ID [1] 0 0
2013-005101-31
Secondary ID [2] 0 0
AV001
Universal Trial Number (UTN)
Trial acronym
Linked study record

Health condition
Health condition(s) or problem(s) studied:
Leukemia, Myelogenous, Chronic, Breakpoint Cluster Region-Abelson Proto-oncogene (BCR-ABL) Positive 0 0
Condition category
Condition code
Cancer 0 0 0 0
Leukaemia - Acute leukaemia
Cancer 0 0 0 0
Leukaemia - Chronic leukaemia
Cancer 0 0 0 0
Children's - Leukaemia & Lymphoma

Intervention/exposure
Study type
Interventional
Description of intervention(s) / exposure
Treatment: Drugs - Bosutinib
Treatment: Drugs - Imatinib

Experimental: Bosutinib - Bosutinib, 400 mg, oral administration once a day

Active comparator: Imatinib - Imatinib, 400 mg, oral administration once a day


Treatment: Drugs: Bosutinib
Bosutinib (Bosulif®) is an orally bioavailable, potent, multi-targeted, dual Src-Abl tyrosine kinase inhibitor (TKI) that has been approved for the treatment of adult patients with Philadelphia positive (Ph+) chronic phase (CP), accelerated phase (AP) and blast phase (BP) chronic myelogenous leukemia (CML) previously treated with other TKI inhibitor therapy.\[1\] This study will investigate the use of bosutinib as first-line treatment for patients with Ph+ CP CML.

Treatment: Drugs: Imatinib
Imatinib mesylate (referred to in this protocol as imatinib) is an inhibitor of the BCR-ABL kinase and been the standard first-line therapy for patients with chronic-phase CML. Imatinib was granted approval by the European Commission in November 2001 and by the FDA in December 2002 for the treatment of newly diagnosed patients with CP Ph+ CML based on results from the IRIS trial.

Imatinib is considered the standard of care for both first-line and later line settings, and consequently is an appropriate active comparator.

Intervention code [1] 0 0
Treatment: Drugs
Comparator / control treatment
Control group

Outcomes
Primary outcome [1] 0 0
Percentage of Participants With Major Molecular Response (MMR) at Month 12
Timepoint [1] 0 0
Month 12
Secondary outcome [1] 0 0
Percentage of Participants With Major Molecular Response (MMR) Up to Month 18
Timepoint [1] 0 0
Up to Month 18
Secondary outcome [2] 0 0
Kaplan-Meier Estimate of Probability of Retaining Major Molecular Response (MMR) at Month 48
Timepoint [2] 0 0
Month 48
Secondary outcome [3] 0 0
Percentage of Participants With Complete Cytogenetic Response (CCyR) Up to Month 12
Timepoint [3] 0 0
Up to Month 12
Secondary outcome [4] 0 0
Kaplan-Meier Estimate of Probability of Retaining Complete Cytogenetic Response (CCyR) at Month 48
Timepoint [4] 0 0
Month 48
Secondary outcome [5] 0 0
Cumulative Incidence of Event Free Survival (EFS) Events
Timepoint [5] 0 0
Up to Month 60
Secondary outcome [6] 0 0
Overall Survival (OS) Rate
Timepoint [6] 0 0
Up to Month 60

Eligibility
Key inclusion criteria
1. Molecular diagnosis of CP CML of = 6 months (from initial diagnosis).
2. Adequate hepatic, renal and pancreatic function.
3. Age = 18 years.
Minimum age
18 Years
Maximum age
No limit
Sex
Both males and females
Can healthy volunteers participate?
No
Key exclusion criteria
1. Any prior medical treatment for CML, including tyrosine kinase inhibitors (TKIs), with the exception of hydroxyurea and/or anagrelide treatment, which are permitted for up to 6 months prior to study entry (signature of ICF) if suitably approved for use in the subject's region.
2. Any past or current Central Nervous System (CNS) involvement, including leptomeningeal leukemia.
3. Extramedullary disease only.
4. Major surgery or radiotherapy within 14 days of randomization.
5. History of clinically significant or uncontrolled cardiac disease.
6. Known seropositivity to human immunodeficiency virus (HIV), current acute or chronic hepatitis B (hepatitis B surface-antigen positive), hepatitis C, cirrhosis or evidence of decompensated liver disease. Patients with resolved Hepatitis B can be included.
7. Recent or ongoing clinically significant GI disorder, e.g. Crohn's Disease, Ulcerative Colitis, or prior total or partial gastrectomy.
8. History of another malignancy within 5 years with the exception of basal cell carcinoma or cervical carcinoma in situ or stage 1 or 2 cancer that is considered adequately treated and currently in complete remission for at least l2 months.
9. Current, or recent (within 30 days, or 5 half-lives of investigational product) participation in other clinical trials of investigational agents and/or containing interventional procedures deemed contrary to the objectives and conduct of this trial.

Study design
Purpose of the study
Treatment
Allocation to intervention
Randomised controlled trial
Procedure for enrolling a subject and allocating the treatment (allocation concealment procedures)
Methods used to generate the sequence in which subjects will be randomised (sequence generation)
Masking / blinding
Open (masking not used)
Who is / are masked / blinded?



Intervention assignment
Parallel
Other design features
Phase
Phase 3
Type of endpoint/s
Statistical methods / analysis

Recruitment
Recruitment status
Completed
Data analysis
Reason for early stopping/withdrawal
Other reasons
Date of first participant enrolment
Anticipated
Actual
Date of last participant enrolment
Anticipated
Actual
Date of last data collection
Anticipated
Actual
Sample size
Target
Accrual to date
Final
Recruitment in Australia
Recruitment state(s)
NSW,VIC
Recruitment hospital [1] 0 0
St George Hospital - Hematology Department - Kogarah
Recruitment hospital [2] 0 0
Eastern Clinical Research Unit, Level 2 - Box Hill
Recruitment postcode(s) [1] 0 0
2217 - Kogarah
Recruitment postcode(s) [2] 0 0
3128 - Box Hill
Recruitment outside Australia
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United States of America
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California
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Georgia
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Hawaii
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Idaho
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Illinois
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Indiana
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United States of America
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Louisiana
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Maryland
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Massachusetts
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Michigan
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Minnesota
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Mississippi
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Nebraska
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New Jersey
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New Mexico
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New York
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North Carolina
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Ohio
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South Carolina
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Utah
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Wisconsin
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Belgium
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Ghent
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Belgium
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Leuven
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Liège
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Verviers
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Quebec
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Canada
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Saskatchewan
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Czechia
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Brno
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Czechia
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Hradec Králové
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Olomouc
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Czechia
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Prague
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Aalborg
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Aarhus
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Roskilde
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RP
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Jena Lobeda-Ost
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Magdeburg
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Györ
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Haifa
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Petah-Tikva
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CT
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Bergamo
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Bologna
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Reggio Calabria
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Roma
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Toledo
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Valencia
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Sweden
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Lund
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Stockholm
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Uppsala
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Taiwan
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Thailand
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Chiang MAI
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Bangkok
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Ukraine
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Ivano-Frankivsk
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Ukraine
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Khmelnytskyi
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Ukraine
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Kyiv
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Ukraine
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Lviv
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United Kingdom
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Greater London
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Merseyside
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Nottinghamshire
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Oxfordshire
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South Yorkshire
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United Kingdom
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WEST Midlands
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United Kingdom
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WEST Yorkshire
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United Kingdom
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Cardiff
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United Kingdom
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Leicester

Funding & Sponsors
Primary sponsor type
Commercial sector/industry
Name
Pfizer
Address
Country

Ethics approval
Ethics application status

Summary
Brief summary
Trial website
Trial related presentations / publications
Public notes

Contacts
Principal investigator
Name 0 0
Pfizer CT.gov Call Center
Address 0 0
Pfizer
Country 0 0
Phone 0 0
Fax 0 0
Email 0 0
Contact person for public queries
Name 0 0
Address 0 0
Country 0 0
Phone 0 0
Fax 0 0
Email 0 0
Contact person for scientific queries

Data sharing statement
Will individual participant data (IPD) for this trial be available (including data dictionaries)?
Yes
What data in particular will be shared?
Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical_trials/trial_data_and_results/data_requests.
When will data be available (start and end dates)?
Available to whom?
Available for what types of analyses?
How or where can data be obtained?
IPD available at link: https://www.pfizer.com/science/clinical_trials/trial_data_and_results/data_requests


What supporting documents are/will be available?

No Supporting Document Provided



Results publications and other study-related documents

No documents have been uploaded by study researchers.