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Trial details imported from ClinicalTrials.gov

For full trial details, please see the original record at https://clinicaltrials.gov/study/NCT03340129




Registration number
NCT03340129
Ethics application status
Date submitted
28/08/2017
Date registered
13/11/2017

Titles & IDs
Public title
Anti-PD 1 Brain Collaboration + Radiotherapy Extension (ABC-X Study)
Scientific title
A Phase II, Open Label, Randomised, Controlled Trial of Ipilimumab and Nivolumab With Concurrent Intracranial Stereotactic Radiotherapy Versus Ipilimumab and Nivolumab Alone in Patients With Melanoma Brain Metastases.
Secondary ID [1] 0 0
MIA2019/CT/258
Universal Trial Number (UTN)
Trial acronym
ABC-X
Linked study record

Health condition
Health condition(s) or problem(s) studied:
Melanoma Stage Iv 0 0
Condition category
Condition code
Cancer 0 0 0 0
Malignant melanoma

Intervention/exposure
Study type
Interventional
Description of intervention(s) / exposure
Treatment: Drugs - Ipilimumab
Treatment: Drugs - Nivolumab
Treatment: Other - Stereotactic Radiotherapy
Other interventions - Salvage therapy

Active comparator: Nivolumab + ipilimumab - Nivolumab 1mg/kg and ipilimumab 3mg/kg Q3W x 4 doses, then nivolumab 480 mg every 4 weeks.

Any form of salvage therapy (surgery or radiotherapy) may be administered to either cohort for the treatment of intracranial disease progression.

Active comparator: Nivolumab + ipilimumab,concurrent SRS - Nivolumab 1mg/kg and ipilimumab 3mg/kg Q3W x 4 doses, then nivolumab 480 mg every 4 weeks.

Stereotactic radiotherapy 16 to 22 Gy in 1 fraction or 24 to 30 Gy, hypofractionated for larger lesions. Stereotactic radiotherapy to commence within 7 days of of the baseline / planning MRI brain. Hypofractionated stereotactic radiotherapy should be completed within 14 day of the first fraction.

Any form of salvage therapy (surgery or radiotherapy) may be administered to either cohort for the treatment of intracranial disease progression.


Treatment: Drugs: Ipilimumab
Ipilimumab 3mg per kg every 3 weeks for 4 doses

Treatment: Drugs: Nivolumab
Nivolumab 1mg/kg every 3 weeks for 4 doses, then 480mg every 4 weeks.

Treatment: Other: Stereotactic Radiotherapy
The first dose of immunotherapy Must be given prior to the start of radiotherapy. One fraction at between 16 to 22 Gy or 24 to 30 Gy hypofractionated for larger lesions.

Other interventions: Salvage therapy
Any form of salvage therapy (surgery or radiotherapy) for intracranial disease progression, further disease control at any site, symptom control or treatment of cerebral haemorrhage or cerebral radionecrosis.

Intervention code [1] 0 0
Treatment: Drugs
Intervention code [2] 0 0
Treatment: Other
Intervention code [3] 0 0
Other interventions
Comparator / control treatment
Control group

Outcomes
Primary outcome [1] 0 0
Neurological specific cause of death
Timepoint [1] 0 0
One year
Secondary outcome [1] 0 0
Intracranial response rate
Timepoint [1] 0 0
Approximately 3 years
Secondary outcome [2] 0 0
Extracranial response rate
Timepoint [2] 0 0
Approximately 5 years
Secondary outcome [3] 0 0
Overall response rate
Timepoint [3] 0 0
Approximately 5 years
Secondary outcome [4] 0 0
Overall progression free survival
Timepoint [4] 0 0
1, 2 and 5 years
Secondary outcome [5] 0 0
Non-Neurological specific cause of death
Timepoint [5] 0 0
1 years
Secondary outcome [6] 0 0
Overall survival
Timepoint [6] 0 0
1, 2 and 5 years.
Secondary outcome [7] 0 0
Incidence of radionecrosis
Timepoint [7] 0 0
5 years
Secondary outcome [8] 0 0
Requirement for salvage radiotherapy
Timepoint [8] 0 0
1 year
Secondary outcome [9] 0 0
Requirement for salvage intracranial surgery
Timepoint [9] 0 0
1 year
Secondary outcome [10] 0 0
Change in neurocognitive function scores
Timepoint [10] 0 0
Approximately 5 years
Secondary outcome [11] 0 0
Description of impaired neurological function and neurological adverse events
Timepoint [11] 0 0
Approximately 5 years
Secondary outcome [12] 0 0
Time to neurological deterioration
Timepoint [12] 0 0
Approximately 5 years
Secondary outcome [13] 0 0
Duration of neurological deterioration
Timepoint [13] 0 0
Approximately 5 years
Secondary outcome [14] 0 0
Patient rated quality of life
Timepoint [14] 0 0
Approximately 5 years
Secondary outcome [15] 0 0
Functional performance status
Timepoint [15] 0 0
Approximately 5 years
Secondary outcome [16] 0 0
Adverse events
Timepoint [16] 0 0
Approximately 5 years
Secondary outcome [17] 0 0
Tissue, blood and gut biomarkers of response, progression and toxicity
Timepoint [17] 0 0
Approximately 5 years

Eligibility
Key inclusion criteria
1. Female or male patients, =18 years of age.
2. Signed, written, informed consent.
3. AJCC Stage IV [any T, any N, M1d (0) or M1D(1)] histologically confirmed cutaneous, acral or mucosal unresectable melanoma or unknown primary melanoma and at least 1 radiological definitive brain metastasis that is = 5mm and =40mm, measurable per RECIST version 1.1 guidelines (modified for brain metastases, enabling up to 5 target lesions in the brain as well as up to 5 extracranial target lesions). There is no upper limit restriction in the number of brain metastases, provided the remaining eligibility criteria are met.
4. The BRAF mutation status must be available prior to randomisation.
5. The treating clinician(s) should consider the intracranial disease amenable to stereotactic radiotherapy over whole brain radiotherapy. Patients for whom there is a definite and immediate indication for radiotherapy (e.g. rapidly progressing disease with associated clinical signs and /or symptoms) should not be considered for enrolment.
6. Brain metastases must be untreated with any modality of radiotherapy or systemic treatment. Previous surgery for melanoma brain metastases is permitted if it resulted in gross total resection and no radiotherapeutic cavity boost was required.
7. No prior systemic treatment for brain metastases is permitted unless given in the neoadjuvant or adjuvant settings for systemic drug the treatment for extracranial disease only. At the time of neoadjuvant or adjuvant systemic therapy for extracranial disease, there should be radiological evidence of the absence of brain metastases. The presenting diagnosis of brain metastases at the time of enrolment in this study must have occurred a minimum of 6 months after stopping neoadjuvant or adjuvant systemic therapy (prior anti PD1, anti PD-L1, anti CTLA-4, BRAF / MEK inhibitors or clinical trial agents) are acceptable in the setting of neoadjuvant or adjuvant treatment
8. Asymptomatic from brain metastases at the time of study enrolment without corticosteroids, analgesia or any other treatment for the management of neurological symptoms (with the exception of antiepileptics prescribed for any reason, provided patient is asymptomatic). Resolved neurological symptoms are permitted if complete resolution, without any intervention, has been sustained for a minimum of 7 days prior to randomisation.
9. Eastern Cooperative Oncology Group (ECOG) Performance Status of 0-2.
10. A life expectancy > 30 days.
11. Able to undergo MRI with Gadolinium contrast agent. CT of the brain is not an acceptable alternative should patients be unable to safely undergo a contrast MRI.
12. Adequate haematological, hepatic and renal organ function as defined by:

1. White cell count = 2.0 × 10x9/L
2. Neutrophil count = 1.5 × 10x9/L
3. Haemoglobin = 90 g/L
4. Platelet count = 100 x 10x9/L
5. Total bilirubin = 1.5 x ULN
6. Alanine transaminase = 3.0 x ULN
7. Aspartate aminotransferase = 3.0 x ULN
8. Serum creatinine = 1.5 x the upper limit of normal (ULN). If serum creatinine is > 1.5 x ULN, calculate creatinine clearance using standard Cockcroft-Gault formula. Creatinine clearance must be 40ml/min to be eligible.
13. Women of childbearing potential (WOCBP) must have a negative serum pregnancy test within 7 days of the first dose of study treatment and agree to use effective contraception from 14 days prior to commencing study treatment, throughout the treatment period and for 23 weeks * after the last dose of study treatment. Effective contraception includes:

1. Intrauterine device with a documented failure rate of less than 1% per year.
2. Vasectomised partner who is sterile prior to the female partner patient's commencement of study treatment and is the sole sexual partner for that female.
3. Combined (oestrogen and progestogen) hormonal contraception associated with inhibition of ovulation or progestogen only hormonal contraception associated with inhibition of ovulation.

Women who are not of childbearing potential are defined as any female who has had a documented hysterectomy, bilateral oophorectomy or bilateral tubal ligation or any female who is post-menopausal (= one year without menses and >50 years of age in the absence of hormone replacement therapy).
14. Men with any female partner of childbearing potential must agree to use effective contraception from 14 days prior to commencing study treatment, throughout the treatment period and for 31 weeks* after the last dose of study treatment. Effective contraception includes:

1. Documented vasectomy and sterility
2. In the partner - intrauterine device with a documented failure rate of less than 1% per year
3. In the female partner - Combined (oestrogen and progestogen) hormonal contraception associated with inhibition of ovulation or progestogen only hormonal contraception associated with inhibition of ovulation.

* These durations have been calculated using the upper limit of the half-life for nivolumab (25 days) and are based on the protocol requirement that WOCBP use contraception for 5 half-lives plus 30 days and men who are sexually active with WOCBP use contraception for 5 half-lives plus 90 days.
Minimum age
18 Years
Maximum age
120 Years
Sex
Both males and females
Can healthy volunteers participate?
No
Key exclusion criteria
Exclusion Criteria

1. Patients whose intracranial disease changes between the diagnostic MRI scan and the baseline / SRS planning MRI scan and who are no longer suitable for SRS and / or require a specific alternative treatment outside of this protocol.
2. Melanoma brain metastasis greater than 40mm.
3. Evidence of leptomeningeal disease, with the exception of pathological findings seen at a previous resection of brain disease, but with no evidence of leptomeningeal disease elsewhere at the time of resection or at study entry.
4. History of, or current ocular melanoma (patients with mucosal and acral melanoma are eligible).
5. Neurological symptoms from brain metastases present at baseline (resolved neurological symptoms, prior to enrolment, are permitted).
6. Prior radiotherapy to the brain (surgery permitted).
7. Prior systemic drug therapy for melanoma, unless given in the neoadjuvant or adjuvant setting and completed 6 months before enrolment in this study.
8. Patients with active, known or suspected autoimmune disease. Patients with the following are permitted to enrol:

1. Vitiligo
2. Type I diabetes mellitus
3. Residual hypothyroidism due to an autoimmune condition only requiring hormone replacement
4. Psoriasis not requiring systemic treatment
5. Autoimmune conditions not expected to recur in the absence of an external trigger.
9. Current systemic treatment with corticosteroids, or within 7 days of randomisation, with the exception of prednisone at non-immunosuppressive doses of = 10 mg/day (or equivalent, e.g. e.g. prednisone 10mg = dexamethasone 1.6mg = hydrocortisone 40mg). Patients with the following circumstances are permitted to enrol:

1. Past treatment for non-neurological symptoms allowed, if this was ceased 7 days prior to randomisation
2. Inhaled or intranasal corticosteroids (with minimal systemic absorption) may be continued if the patient is on a stable dose
3. Non-absorbed intra-articular steroid injections.

During the study, treatment with systemic corticosteroids is permitted during radiotherapy if the patient experiences radiation related symptoms but this should be tapered per standard clinical practice as soon as possible and before the next infusion of study drug is due. This also refers to steroids for drug related signs or symptoms.
10. Any active infection requiring treatment.
11. A history of interstitial lung disease.
12. Any concurrent malignancy requiring any treatment or a history of another malignancy, unless the patient has been disease-free for 3 years.
13. Serious or unstable pre-existing medical conditions or other conditions that could interfere with the patient's safety, consent, or compliance.
14. Pregnant or breastfeeding females.
15. Administration of any form of live vaccine within 30 days of starting the trial and during the trial. Administration of any other vaccine is cautionary within 30 days of starting the trial and for the duration of the treatment phase of the trial.

Study design
Purpose of the study
Treatment
Allocation to intervention
Randomised controlled trial
Procedure for enrolling a subject and allocating the treatment (allocation concealment procedures)
Methods used to generate the sequence in which subjects will be randomised (sequence generation)
Masking / blinding
Open (masking not used)
Who is / are masked / blinded?



Intervention assignment
Parallel
Other design features
Phase
Phase 2
Type of endpoint/s
Statistical methods / analysis

Recruitment
Recruitment status
Recruiting
Data analysis
Reason for early stopping/withdrawal
Other reasons
Date of first participant enrolment
Anticipated
Actual
Date of last participant enrolment
Anticipated
Actual
Date of last data collection
Anticipated
Actual
Sample size
Target
Accrual to date
Final
Recruitment in Australia
Recruitment state(s)
NSW,QLD,SA,VIC
Recruitment hospital [1] 0 0
Westmead Hospital - Sydney
Recruitment hospital [2] 0 0
Calvary Mater NewcastleHospital - Waratah
Recruitment hospital [3] 0 0
Melanoma Institute Australia - Wollstonecraft
Recruitment hospital [4] 0 0
Princess Alexandra Hospital - Woolloongabba
Recruitment hospital [5] 0 0
Royal Adelaide Hospital - Adelaide
Recruitment hospital [6] 0 0
Peter MacCallum Cancer Centre - East Melbourne
Recruitment hospital [7] 0 0
Alfred Hospital - Melbourne
Recruitment postcode(s) [1] 0 0
2145 - Sydney
Recruitment postcode(s) [2] 0 0
2298 - Waratah
Recruitment postcode(s) [3] 0 0
2065 - Wollstonecraft
Recruitment postcode(s) [4] 0 0
4102 - Woolloongabba
Recruitment postcode(s) [5] 0 0
5000 - Adelaide
Recruitment postcode(s) [6] 0 0
3002 - East Melbourne
Recruitment postcode(s) [7] 0 0
3004 - Melbourne
Recruitment outside Australia
Country [1] 0 0
Norway
State/province [1] 0 0
Oslo

Funding & Sponsors
Primary sponsor type
Other
Name
Melanoma Institute Australia
Address
Country
Other collaborator category [1] 0 0
Commercial sector/industry
Name [1] 0 0
Bristol-Myers Squibb
Address [1] 0 0
Country [1] 0 0

Ethics approval
Ethics application status

Summary
Brief summary
Trial website
Trial related presentations / publications
Public notes

Contacts
Principal investigator
Name 0 0
Georgina V Long, MBBS PhD
Address 0 0
Melanoma Institute Australia
Country 0 0
Phone 0 0
Fax 0 0
Email 0 0
Contact person for public queries
Name 0 0
Georgina V Long, MBBS PhD
Address 0 0
Country 0 0
Phone 0 0
+61 2 9911 7200
Fax 0 0
Email 0 0
Contact person for scientific queries

Data sharing statement
Will individual participant data (IPD) for this trial be available (including data dictionaries)?
No
No/undecided IPD sharing reason/comment


What supporting documents are/will be available?

No Supporting Document Provided



Results publications and other study-related documents

No documents have been uploaded by study researchers.