The ANZCTR website will be unavailable from 1pm until 3pm (AEDT) on Wednesday the 30th of October for website maintenance. Please be sure to log out of the system in order to avoid any loss of data.

The safety and scientific validity of this study is the responsibility of the study sponsor and investigators. Listing a study does not mean it has been endorsed by the ANZCTR. Before participating in a study, talk to your health care provider and refer to this information for consumers
Trial details imported from ClinicalTrials.gov

For full trial details, please see the original record at https://clinicaltrials.gov/study/NCT03439488




Registration number
NCT03439488
Ethics application status
Date submitted
23/01/2018
Date registered
20/02/2018
Date last updated
10/12/2019

Titles & IDs
Public title
A Study of Orally Administered JNJ-440 to Evaluate the Safety, Tolerability, and Pharmacokinetics After Single Ascending Doses Including Food Effect Evaluation; After Multi-Day Dosing in Healthy Participants; and After Multiple (Ascending) Doses in Participants With Chronic Hepatitis B
Scientific title
A Multipart Phase 1, Double-Blind, Randomized, Placebo-Controlled, First-in-Human, Study of Orally Administered JNJ-440 to Evaluate the Safety, Tolerability, and Pharmacokinetics After Single Ascending Doses Including Food Effect Evaluation (Part 1); After Multi-Day Dosing (Part 2) in Healthy Subjects; and After Multiple (Ascending) Doses in Subjects With Chronic Hepatitis B (Part 3)
Secondary ID [1] 0 0
JNJ-440-1301
Secondary ID [2] 0 0
JNJ-440-1301
Universal Trial Number (UTN)
Trial acronym
Linked study record

Health condition
Health condition(s) or problem(s) studied:
Chronic Hepatitis B 0 0
Condition category
Condition code
Infection 0 0 0 0
Other infectious diseases
Oral and Gastrointestinal 0 0 0 0
Other diseases of the mouth, teeth, oesophagus, digestive system including liver and colon

Intervention/exposure
Study type
Interventional
Description of intervention(s) / exposure
Treatment: Drugs - JNJ-440
Treatment: Drugs - Placebo

Experimental: Part 1 (Healthy Participants): Single Ascending Dose (SAD) - Participants in Cohorts 1 to 5 and 3 optional cohorts (Cohorts 6, 7 and 10) will receive a single dose of JNJ-440/placebo on Day 1. Two cohorts will receive a second dose of JNJ-440/placebo in a fed state (participants from Cohort 3 will also participate in Cohort 8) or as an alternative JNJ-440 formulation (participants from Cohort 2 will also participate in optional Cohort 9) after a washout window of at least 10 days. In Cohorts 1 to 4, study drug will be administered under fasted conditions; in the remaining cohorts, study drug will be administered under fasted/fed conditions depending on the results of the food effect evaluation.

Experimental: Part 2 (Healthy Participants): Multiple Ascending Dose (MAD) - Participants in Cohorts 1 and 2 will receive a once daily dose of JNJ-440/placebo for the duration of 7 days under fasted or fed conditions. Participants in an optional cohort (Cohort 3) may receive a once daily or twice daily dose of JNJ-440/placebo for the duration of 7 or 14 days under fasted or fed conditions. The starting dose for Cohort 1 in Part 2 will be determined by the Sponsor in consultation with the Principal Investigator based on the data from Part 1. Dose escalation will be performed only after review of safety and pharmacokinetic (PK) data after a minimum of 7 days of study drug administration.

Experimental: Part 3 (Chronic Hepatitis B [CHB] Participants): MAD - Participants in Cohorts 1 and 2 and 3 optional cohorts (Cohorts 3, 4, and 5) will receive multiple ascending doses of JNJ-440/placebo once daily or twice daily for 28 days under fed or fasted conditions. The starting dose and formulation for Cohort 1 will be determined based on the review of available data in healthy participants from Part 1 (SAD) and Part 2 (MAD). Dose escalation will be performed only after review of safety, tolerability, and PK data after a minimum of 14 days of study drug administration from at least 8 CHB participants.


Treatment: Drugs: JNJ-440
JNJ-440 will be administered as oral tablets in Parts 1, 2 and 3. JNJ-440 may be provided as oral solution in a cohort in Part 1.

Treatment: Drugs: Placebo
Matching placebo as oral tablets will be administered in Parts 1, 2 and 3.

Intervention code [1] 0 0
Treatment: Drugs
Comparator / control treatment
Control group

Outcomes
Primary outcome [1] 0 0
Parts 1, 2, and 3: Number of Participants With Adverse Events (AEs) as a Measure of Safety and Tolerability
Timepoint [1] 0 0
Approximately up to 8 weeks
Primary outcome [2] 0 0
Parts 1, 2, and 3: Number of Participants With Clinically Significant Changes in Physical Examination (Body Weight Measurement and Skin Examination)
Timepoint [2] 0 0
Approximately up to 8 weeks
Primary outcome [3] 0 0
Parts 1, 2, and 3: Number of Participants With Clinically Significant Changes in Vital Signs
Timepoint [3] 0 0
Approximately up to 8 weeks
Primary outcome [4] 0 0
Parts 1, 2, and 3: Number of Participants With ECG Abnormalities
Timepoint [4] 0 0
Approximately up to 8 weeks
Primary outcome [5] 0 0
Parts 1, 2, and 3: Number of Participants With Holter Monitoring Abnormalities
Timepoint [5] 0 0
Up to 24 hours post-dose on Day 1
Primary outcome [6] 0 0
Parts 1, 2, and 3: Number of Participants With Clinical Laboratory Abnormalities
Timepoint [6] 0 0
Approximately up to 8 weeks
Primary outcome [7] 0 0
Part 1: Maximum Observed Plasma Concentration (Cmax)
Timepoint [7] 0 0
Day 1 (predose and at 0.5, 1, 2, 3, 4, 6, 8, 10, 12, 18, 24, 36, 48, 72, 96, and 120 hours postdose)
Primary outcome [8] 0 0
Part 1: Area Under the Plasma Concentration-Time Curve From Time Zero to Last Quantifiable Time (AUC [0-last])
Timepoint [8] 0 0
Day 1 (predose and at 0.5, 1, 2, 3, 4, 6, 8, 10, 12, 18, 24, 36, 48, 72, 96, and 120 hours postdose)
Primary outcome [9] 0 0
Part 1: Area Under the Plasma Concentration-Time Curve From Time Zero to Infinite Time (AUC[0-infinity])
Timepoint [9] 0 0
Day 1 (predose and at 0.5, 1, 2, 3, 4, 6, 8, 10, 12, 18, 24, 36, 48, 72, 96, and 120 hours postdose)
Primary outcome [10] 0 0
Part 3: Maximum Observed Plasma Concentration (Cmax)
Timepoint [10] 0 0
Day 1 (predose, and at 0.5, 1, 2, 4, 8, and 12 hours post dose), morning predose on Days 2, 15 and 21, and Day 28 (predose, and at 0.5, 1, 2, 4, 8, and 12 hours postdose; 24 hours postdose [once daily {QD} dosing only])
Primary outcome [11] 0 0
Part 3: Observed Plasma Concentration From Time 0 to tau Hours Postdose (C[0-tau])
Timepoint [11] 0 0
Day 1 (predose, and at 0.5, 1, 2, 4, 8, and 12 hours post dose), morning predose on Days 2, 15 and 21, and Day 28 (predose, and at 0.5, 1, 2, 4, 8, and 12 hours postdose; 24 hours postdose [QD dosing only])
Primary outcome [12] 0 0
Part 3: Area Under the Curve From Time Zero to End of Dosing Interval (AUC[0-tau])
Timepoint [12] 0 0
Day 1 (predose, and at 0.5, 1, 2, 4, 8, and 12 hours post dose), morning predose on Days 2, 15 and 21, and Day 28 (predose, and at 0.5, 1, 2, 4, 8, and 12 hours postdose; 24 hours postdose [QD dosing only])
Secondary outcome [1] 0 0
Part 1: Ratio of Cmax Values Between Test and Reference Ratio (Cmax, test/reference) for Different Dosage Forms
Timepoint [1] 0 0
Day 1 (predose and at 0.5, 1, 2, 3, 4, 6, 8, 10, 12, 18, 24, 36, 48, 72, 96, and 120 hours postdose)
Secondary outcome [2] 0 0
Part 1: Ratio of AUC(0-last) Values Between Test and Reference (Ratio AUC[0-last],test/reference) for Different Dosage Forms
Timepoint [2] 0 0
Day 1 (predose and at 0.5, 1, 2, 3, 4, 6, 8, 10, 12, 18, 24, 36, 48, 72, 96, and 120 hours postdose)
Secondary outcome [3] 0 0
Part 1: Ratio of AUC(0-infinity) Values Between Test and Reference (Ratio AUC[0-infinity], test/reference) for Different Dosage Forms
Timepoint [3] 0 0
Day 1 (predose and at 0.5, 1, 2, 3, 4, 6, 8, 10, 12, 18, 24, 36, 48, 72, 96, and 120 hours postdose)
Secondary outcome [4] 0 0
Part 1: Ratio of Cmax Values Between Fed and Fasted (Ratio Cmax, test/reference) Conditions
Timepoint [4] 0 0
Day 1 (predose and at 0.5, 1, 2, 3, 4, 6, 8, 10, 12, 18, 24, 36, 48, 72, 96, and 120 hours postdose)
Secondary outcome [5] 0 0
Part 1: Ratio of AUC(0-last) Values Between Fed and Fasted (Ratio AUC[0- last],test/reference)
Timepoint [5] 0 0
Day 1 (predose and at 0.5, 1, 2, 3, 4, 6, 8, 10, 12, 18, 24, 36, 48, 72, 96, and 120 hours postdose)
Secondary outcome [6] 0 0
Part 1: Ratio of AUC(0-infinity) Values Between Fed and Fasted (Ratio AUC[0-infinity], test/reference)
Timepoint [6] 0 0
Day 1 (predose and at 0.5, 1, 2, 3, 4, 6, 8, 10, 12, 18, 24, 36, 48, 72, 96, and 120 hours postdose)
Secondary outcome [7] 0 0
Part 3: Mean Change from Baseline in HBV DNA Levels
Timepoint [7] 0 0
Baseline up to Day 56
Secondary outcome [8] 0 0
Part 3: Percentage of Participants with HBV DNA Levels and Undetectable HBV DNA
Timepoint [8] 0 0
Baseline up to Day 56
Secondary outcome [9] 0 0
Part 3: Change From Baseline in Hepatitis B Surface Antigen (HBsAg) Levels
Timepoint [9] 0 0
Baseline up to Day 56
Secondary outcome [10] 0 0
Part 3: Change From Baseline in Hepatitis B e Antigen (HBeAg) Levels
Timepoint [10] 0 0
Baseline up to Day 56
Secondary outcome [11] 0 0
Part 3: Relationship Between Plasma Concentration and Antiviral Activity
Timepoint [11] 0 0
Up to Day 56
Secondary outcome [12] 0 0
Part 3: Relationship Between Plasma Concentration and Select AEs or Laboratory Changes
Timepoint [12] 0 0
Up to Day 56
Secondary outcome [13] 0 0
Part 3: Change From Baseline in HBV DNA (Antiviral Activity) in Chronic Hepatitis B (CHB) Participants with Sequence Variations in the HBV Genome
Timepoint [13] 0 0
Baseline up to Day 56
Secondary outcome [14] 0 0
Part 3: Number of Participants with Emergence of Treatment Associated Mutations in the HBV Genome
Timepoint [14] 0 0
Baseline up to Day 29
Secondary outcome [15] 0 0
Parts 1, 2, and 3: Relationship Between JNJ-440 Plasma Concentrations and Time-Matched Change from Baseline QTcF
Timepoint [15] 0 0
Approximately up to 18 weeks

Eligibility
Key inclusion criteria
Inclusion Criteria for Healthy Participants:

* Female participants (except for postmenopausal women) must have a negative pregnancy test at screening and on Day -1
* Participants must have a body mass index (BMI; weight in kilogram [kg] divided by the square of height in meters) of 18.0 to 30.0 kilogram per meter square (kg/m^2), extremes included
* Participants must agree not to donate blood during the study and for at least 1 month after the completion of study drug administration

Inclusion Criteria for Participants with Chronic Hepatitis B (CHB):

* Participant must have CHB infection documented by: (a) Serum hepatitis B surface antigen (HBsAg) positive at screening and at least 6 months prior to screening; (b) Serum antibody immunoglobulin M (IgM) anti-HBc antibody negative at screening
* Participants must currently not be receiving any CHB treatment at screening, that is, have never received treatment with hepatitis B virus (HBV) antiviral medicines, nucleos(t)ide analog (NAs), interferon (IFN) products, or investigational anti-HBV agents, OR Have not been on treatment with HBV antiviral medicines, NAs, or IFN products within 6 months prior to baseline (first intake of study drugs)
Minimum age
18 Years
Maximum age
55 Years
Sex
Both males and females
Can healthy volunteers participate?
Yes
Key exclusion criteria
Exclusion Criteria for Healthy Participants:

* Participants with a past history of cardiac arrhythmias (example, extrasystoli, tachycardia at rest), history of risk factors for Torsade de Pointes syndrome (example, hypokalemia, family history of long QT Syndrome) or history or other clinical evidence of significant or unstable cardiac disease (example, angina, congestive heart failure, myocardial infarction, diastolic dysfunction, significant arrhythmia, coronary heart disease, and/or clinically significant electrocardiogram [ECG] abnormalities), moderate to severe valvular disease or uncontrolled hypertension at screening. Any evidence of heart block or bundle branch block is also exclusionary
* Participants with any history of confirmed clinically significant skin disease such as, but not limited to, dermatitis, eczema, drug rash, psoriasis, food allergy, and urticarial
* Participants with a history of confirmed clinically significant drug allergy such as, but not limited to, sulfonamides and penicillins, or drug allergy witnessed in previous studies with experimental drugs

Exclusion Criteria for Participants with CHB:

* Participant with positivity of anti-HBs antibodies
* Participants with current hepatitis D virus (HDV) infection (confirmed by HDV antibody) at screening

Study design
Purpose of the study
Other
Allocation to intervention
Randomised controlled trial
Procedure for enrolling a subject and allocating the treatment (allocation concealment procedures)
Methods used to generate the sequence in which subjects will be randomised (sequence generation)
Masking / blinding
Blinded (masking used)
Who is / are masked / blinded?
The people receiving the treatment/s

The people assessing the outcomes
The people analysing the results/data
Intervention assignment
Other
Other design features
Phase
Phase 1
Type of endpoint/s
Statistical methods / analysis

Recruitment
Recruitment status
Completed
Data analysis
Reason for early stopping/withdrawal
Other reasons
Date of first participant enrolment
Anticipated
Actual
Date of last participant enrolment
Anticipated
Actual
Date of last data collection
Anticipated
Actual
Sample size
Target
Accrual to date
Final
Recruitment in Australia
Recruitment state(s)
Recruitment outside Australia
Country [1] 0 0
Korea, Republic of
State/province [1] 0 0
Seoul
Country [2] 0 0
Moldova, Republic of
State/province [2] 0 0
Chisnau
Country [3] 0 0
New Zealand
State/province [3] 0 0
Auckland
Country [4] 0 0
Thailand
State/province [4] 0 0
Bangkok
Country [5] 0 0
Thailand
State/province [5] 0 0
Khon Kaen
Country [6] 0 0
Ukraine
State/province [6] 0 0
Kapitanavka

Funding & Sponsors
Primary sponsor type
Commercial sector/industry
Name
Alios Biopharma Inc.
Address
Country

Ethics approval
Ethics application status

Summary
Brief summary
Trial website
Trial related presentations / publications
Public notes

Contacts
Principal investigator
Name 0 0
Jeysen Yogaratnam
Address 0 0
Alios Biopharma Inc.
Country 0 0
Phone 0 0
Fax 0 0
Email 0 0
Contact person for public queries
Name 0 0
Address 0 0
Country 0 0
Phone 0 0
Fax 0 0
Email 0 0
Contact person for scientific queries

No information has been provided regarding IPD availability


What supporting documents are/will be available?

No Supporting Document Provided



Results publications and other study-related documents

No documents have been uploaded by study researchers.